review article | Q7318358 |
scholarly article | Q13442814 |
P356 | DOI | 10.1517/14712598.4.7.1093 |
P698 | PubMed publication ID | 15268676 |
P2093 | author name string | Terence R Flotte | |
Thomas J Conlon | |||
P2860 | cites work | Mutational analysis of the adeno-associated virus type 2 (AAV2) capsid gene and construction of AAV2 vectors with altered tropism | Q24515072 |
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Dysferlin, a novel skeletal muscle gene, is mutated in Miyoshi myopathy and limb girdle muscular dystrophy | Q28281738 | ||
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In vitro selection of viral vectors with modified tropism: the adeno-associated virus display | Q33187644 | ||
Repeat transduction in the mouse lung by using adeno-associated virus vectors with different serotypes | Q33793801 | ||
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Efficient and selective AAV2-mediated gene transfer directed to human vascular endothelial cells | Q34090326 | ||
The VP1 capsid protein of adeno-associated virus type 2 is carrying a phospholipase A2 domain required for virus infectivity | Q34124491 | ||
A p5 integration efficiency element mediates Rep-dependent integration into AAVS1 at chromosome 19. | Q34156171 | ||
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Effect of DNA-dependent protein kinase on the molecular fate of the rAAV2 genome in skeletal muscle | Q35054512 | ||
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From virus evolution to vector revolution: use of naturally occurring serotypes of adeno-associated virus (AAV) as novel vectors for human gene therapy | Q35180997 | ||
Trans-splicing vectors expand the utility of adeno-associated virus for gene therapy | Q35799349 | ||
Site-specific integration by adeno-associated virus is directed by a cellular DNA sequence | Q35829692 | ||
Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein | Q35943644 | ||
Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus | Q36159178 | ||
Studies of small DNA viruses found in various adenovirus preparations: physical, biological, and immunological characteristics | Q36460379 | ||
DNA-dependent PK inhibits adeno-associated virus DNA integration | Q36604872 | ||
Sustained secretion of human alpha-1-antitrypsin from murine muscle transduced with adeno-associated virus vectors | Q36734619 | ||
Humoral immunity to adeno-associated virus type 2 vectors following administration to murine and nonhuman primate muscle | Q39589663 | ||
Infectious entry pathway of adeno-associated virus and adeno-associated virus vectors | Q39589898 | ||
Enhancement of muscle gene delivery with pseudotyped adeno-associated virus type 5 correlates with myoblast differentiation. | Q39606539 | ||
Ubiquitination of both adeno-associated virus type 2 and 5 capsid proteins affects the transduction efficiency of recombinant vectors. | Q39682659 | ||
Infection of purified nuclei by adeno-associated virus 2. | Q40775943 | ||
Targeted adeno-associated virus vector transduction of nonpermissive cells mediated by a bispecific F(ab'gamma)2 antibody | Q40969562 | ||
Adeno-associated virus vector gene expression occurs in nondividing cells in the absence of vector DNA integration | Q41431346 | ||
Gene expression from adeno-associated virus vectors in airway epithelial cells | Q41606833 | ||
Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector. | Q41722852 | ||
Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain | Q42280576 | ||
Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors | Q43716886 | ||
Intramuscular administration of recombinant adeno-associated virus 2 alpha-1 antitrypsin (rAAV-SERPINA1) vectors in a nonhuman primate model: safety and immunologic aspects | Q44136395 | ||
Efficient trans-splicing in the retina expands the utility of adeno-associated virus as a vector for gene therapy. | Q44305893 | ||
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Recombinant adeno-associated virus-mediated alpha-1 antitrypsin gene therapy prevents type I diabetes in NOD mice | Q44719693 | ||
Transgene expression after rep-mediated site-specific integration into chromosome 19. | Q45019591 | ||
Genetic modifications of the adeno-associated virus type 2 capsid reduce the affinity and the neutralizing effects of human serum antibodies | Q45709087 | ||
Adeno-associated virus terminal repeat (TR) mutant generates self-complementary vectors to overcome the rate-limiting step to transduction in vivo | Q45709105 | ||
Structure determination of adeno-associated virus 2: three complete virus particles per asymmetric unit | Q45723313 | ||
Stable therapeutic serum levels of human alpha-1 antitrypsin (AAT) after portal vein injection of recombinant adeno-associated virus (rAAV) vectors | Q45735547 | ||
Overcoming adeno-associated virus vector size limitation through viral DNA heterodimerization | Q45742577 | ||
Quantitative analysis of the packaging capacity of recombinant adeno-associated virus | Q45766162 | ||
Phenotype correction of hemophilia A mice by spliceosome-mediated RNA trans-splicing | Q45863479 | ||
Targeted transgene integration into transgenic mouse fibroblasts carrying the full-length human AAVS1 locus mediated by HSV/AAV rep(+) hybrid amplicon vector. | Q45864772 | ||
P433 | issue | 7 | |
P407 | language of work or name | English | Q1860 |
P921 | main subject | gene therapy | Q213901 |
vector-borne disease | Q2083837 | ||
P304 | page(s) | 1093-1101 | |
P577 | publication date | 2004-07-01 | |
P1433 | published in | Expert Opinion on Biological Therapy | Q5421201 |
P1476 | title | Recombinant adeno-associated virus vectors for gene therapy | |
P478 | volume | 4 |
Q33864423 | A shortened adeno-associated virus expression cassette for CFTR gene transfer to cystic fibrosis airway epithelia. |
Q34843762 | A simple method to increase the transduction efficiency of single-stranded adeno-associated virus vectors in vitro and in vivo. |
Q40205113 | Adeno-associated virus 2-mediated gene transfer: role of a cellular serine/threonine protein phosphatase in augmenting transduction efficiency |
Q34795088 | Capsid serotype and timing of injection determines AAV transduction in the neonatal mice brain |
Q35636782 | Effect of human vasoactive intestinal peptide gene transfer in a murine model of Sjogren's syndrome |
Q35638200 | Experience with experimental biological treatment and local gene therapy in Sjogren's syndrome: implications for exocrine pathogenesis and treatment |
Q80448411 | Gene therapy for arthritis |
Q36751590 | Gene therapy for type 1 diabetes: is it ready for the clinic? |
Q36240196 | Gene therapy progress and prospects: reprograming gene expression by trans-splicing |
Q35014865 | Hybrid adeno-associated viral vectors utilizing transposase-mediated somatic integration for stable transgene expression in human cells |
Q45862137 | Intraperitoneal gene therapy by rAAV provides long-term survival against epithelial ovarian cancer independently of survivin pathway |
Q45863257 | NOD mouse model for Sjögren's syndrome: lack of longitudinal stability |
Q33832799 | Optimized adeno-associated virus (AAV)-protein phosphatase-5 helper viruses for efficient liver transduction by single-stranded AAV vectors: therapeutic expression of factor IX at reduced vector doses |
Q36144935 | Recombinant adeno-associated virus vectors induce functionally impaired transgene product-specific CD8+ T cells in mice |
Q45370683 | Recombinant adeno-associated virus-mediated gene transfer for the potential therapy of adenosine deaminase-deficient severe combined immune deficiency. |
Q37005491 | Role of cellular FKBP52 protein in intracellular trafficking of recombinant adeno-associated virus 2 vectors |
Q35972733 | Self-Complementary Adeno-Associated Virus Vectors Improve Transduction Efficiency of Corneal Endothelial Cells |
Q38692453 | Somatic correction of junctional epidermolysis bullosa by a highly recombinogenic AAV variant. |
Q39979752 | Strategies for improving the transduction efficiency of single-stranded adeno-associated virus vectors in vitro and in vivo |
Q36966036 | The promise of gene therapy for the treatment of alpha-1 antitrypsin deficiency |
Q42582773 | Treatment of glioblastoma multiforme cells with temozolomide-BioShuttle ligated by the inverse Diels-Alder ligation chemistry |
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