scholarly article | Q13442814 |
P50 | author | Jeffrey Morin | Q61142628 |
Joseph F Nabhan | Q81346655 | ||
Renea Gooch | Q83272755 | ||
P2093 | author name string | Christine E Bulawa | |
Timothy P LaBranche | |||
Kristy M Wood | |||
Surya Bhamidipaty | |||
Varada P Rao | |||
Braydon C Guild | |||
Fazli Bozal | |||
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Frataxin is reduced in Friedreich ataxia patients and is associated with mitochondrial membranes | Q28249379 | ||
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Mouse models for Friedreich ataxia exhibit cardiomyopathy, sensory nerve defect and Fe-S enzyme deficiency followed by intramitochondrial iron deposits | Q28505173 | ||
Modified mRNA directs the fate of heart progenitor cells and induces vascular regeneration after myocardial infarction | Q30580723 | ||
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Human frataxin activates Fe-S cluster biosynthesis by facilitating sulfur transfer chemistry | Q34434217 | ||
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A TAT-frataxin fusion protein increases lifespan and cardiac function in a conditional Friedreich's ataxia mouse model | Q35770976 | ||
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Expression kinetics of nucleoside-modified mRNA delivered in lipid nanoparticles to mice by various routes | Q36218294 | ||
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Improving the endosomal escape of cell-penetrating peptides and their cargos: strategies and challenges | Q37277330 | ||
The pathogenesis of Friedreich ataxia and the structure and function of frataxin | Q37414028 | ||
Friedreich ataxia: metal dysmetabolism in dorsal root ganglia | Q37485501 | ||
The dorsal root ganglion under attack: the acquired sensory ganglionopathies | Q37811641 | ||
Design of multifunctional non-viral gene vectors to overcome physiological barriers: dilemmas and strategies | Q37907456 | ||
Animal and cellular models of Friedreich ataxia. | Q38121944 | ||
Cardiomyopathy of Friedreich ataxia | Q38121946 | ||
P275 | copyright license | Creative Commons Attribution 4.0 International | Q20007257 |
P6216 | copyright status | copyrighted | Q50423863 |
P407 | language of work or name | English | Q1860 |
P921 | main subject | nanoparticle | Q61231 |
Friedreich ataxia | Q913856 | ||
P304 | page(s) | 20019 | |
P577 | publication date | 2016-02-17 | |
P1433 | published in | Scientific Reports | Q2261792 |
P1476 | title | Intrathecal delivery of frataxin mRNA encapsulated in lipid nanoparticles to dorsal root ganglia as a potential therapeutic for Friedreich's ataxia | |
P478 | volume | 6 |
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