scholarly article | Q13442814 |
P50 | author | Yoichi Ishitsuka | Q73209250 |
Muneaki Matsuo | Q87702543 | ||
P2093 | author name string | Tetsumi Irie | |
Hidetoshi Arima | |||
Hirohito Doi | |||
Junya Eto | |||
Koki Shraishi | |||
Koki Wada | |||
Miyuki Maeda | |||
Sakiko Mochinaga | |||
Tatsuhiro Mizoguchi | |||
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Niemann-Pick disease type C | Q21202883 | ||
2-hydroxypropyl-beta-cyclodextrin raises hearing threshold in normal cats and in cats with Niemann-Pick type C disease | Q24598867 | ||
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Miglustat treatment may reduce cerebrospinal fluid levels of the axonal degeneration marker tau in niemann-pick type C. | Q36433310 | ||
Effects of cyclodextrin in two patients with Niemann-Pick Type C disease | Q40265254 | ||
Genetic and chemical correction of cholesterol accumulation and impaired autophagy in hepatic and neural cells derived from Niemann-Pick Type C patient-specific iPS cells. | Q40473012 | ||
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The pharmacokinetics of beta-cyclodextrin and hydroxypropyl-beta-cyclodextrin in the rat | Q70291442 | ||
P407 | language of work or name | English | Q1860 |
P304 | page(s) | 391-400 | |
P577 | publication date | 2014-09-17 | |
P1433 | published in | Molecular Genetics and Metabolism Reports | Q27725363 |
P1476 | title | Effects of intracerebroventricular administration of 2-hydroxypropyl-β-cyclodextrin in a patient with Niemann-Pick Type C disease | |
P478 | volume | 1 |