Efficient hepatic delivery and expression from a recombinant adeno-associated virus 8 pseudotyped alpha1-antitrypsin vector

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Efficient hepatic delivery and expression from a recombinant adeno-associated virus 8 pseudotyped alpha1-antitrypsin vector is …
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scholarly articleQ13442814

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P356DOI10.1016/J.YMTHE.2005.05.016
P698PubMed publication ID16085464
P5875ResearchGate publication ID7675618

P50authorMartha Campbell-ThompsonQ37381204
P2093author name stringSihong Song
Terence R Flotte
Kirsten Erger
Thomas J Conlon
Travis Cossette
Young-Kook Choi
James Crawford
Tracy Clarke
Marda Scott-Jorgensen
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Rapid uncoating of vector genomes is the key to efficient liver transduction with pseudotyped adeno-associated virus vectorsQ36509889
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A novel SV40-based vector successfully transduces and expresses an alpha 1-antitrypsin ribozyme in a human hepatoma-derived cell lineQ40952202
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Stable therapeutic serum levels of human alpha-1 antitrypsin (AAT) after portal vein injection of recombinant adeno-associated virus (rAAV) vectorsQ45735547
Efficient ex vivo transduction of pancreatic islet cells with recombinant adeno-associated virus vectorsQ45738268
Detection of infectious adeno-associated virus particles in human cervical biopsiesQ45754547
Ex vivo and in vivo gene transfer to the skin using replication-deficient recombinant adenovirus vectorsQ45872692
Use of a highly purified alpha 1-antitrypsin standard to establish ranges for the common normal and deficient alpha 1-antitrypsin phenotypesQ46455576
Evaluation of the S-type of alpha-1-antitrypsin as an in vivo and in vitro inhibitor of neutrophil elastaseQ68090902
Augmentation of lung antineutrophil elastase capacity with recombinant human alpha-1-antitrypsinQ68834674
P433issue5
P921main subjectvector-borne diseaseQ2083837
P304page(s)867-875
P577publication date2005-08-08
P1433published inMolecular TherapyQ15762400
P1476titleEfficient hepatic delivery and expression from a recombinant adeno-associated virus 8 pseudotyped alpha1-antitrypsin vector
P478volume12