| scholarly article | Q13442814 |
| P356 | DOI | 10.1007/978-1-4939-7522-8_11 |
| P698 | PubMed publication ID | 29188512 |
| P50 | author | Ivana Trapani | Q57306425 |
| P2093 | author name string | Ivana Trapani | |
| P2860 | cites work | A photoreceptor cell-specific ATP-binding transporter gene (ABCR) is mutated in recessive Stargardt macular dystrophy | Q24324625 |
| Promising and delivering gene therapies for vision loss | Q27007079 | ||
| Gene therapy of inherited retinal degenerations: prospects and challenges | Q27009261 | ||
| Insights into the function of Rim protein in photoreceptors and etiology of Stargardt's disease from the phenotype in abcr knockout mice | Q28140171 | ||
| A hybrid vector system expands adeno-associated viral vector packaging capacity in a transgene-independent manner | Q28256353 | ||
| Isolation of highly infectious and pure adeno-associated virus type 2 vectors with a single-step gravity-flow column. | Q31934499 | ||
| Establishment of an AAV Reverse Infection-Based Array | Q33728191 | ||
| CD40 ligand-dependent activation of cytotoxic T lymphocytes by adeno-associated virus vectors in vivo: role of immature dendritic cells | Q33810726 | ||
| Defective lipid transport and biosynthesis in recessive and dominant Stargardt macular degeneration | Q34157723 | ||
| Efficient transgene reconstitution with hybrid dual AAV vectors carrying the minimized bridging sequences | Q34511733 | ||
| Vector platforms for gene therapy of inherited retinopathies. | Q34561531 | ||
| AAV-mediated photoreceptor transduction of the pig cone-enriched retina | Q35092093 | ||
| Trans-splicing vectors expand the utility of adeno-associated virus for gene therapy | Q35799349 | ||
| The Rd8 mutation of the Crb1 gene is present in vendor lines of C57BL/6N mice and embryonic stem cells, and confounds ocular induced mutant phenotypes | Q36035008 | ||
| Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors | Q36099346 | ||
| Gene therapy of inherited retinopathies: a long and successful road from viral vectors to patients | Q36147481 | ||
| Let There Be Light: Gene and Cell Therapy for Blindness | Q36654534 | ||
| Retinal gene therapy with a large MYO7A cDNA using adeno-associated virus | Q36808032 | ||
| AAV2/8 vectors purified from culture medium with a simple and rapid protocol transduce murine liver, muscle, and retina efficiently | Q37406911 | ||
| Dual adeno-associated virus vectors result in efficient in vitro and in vivo expression of an oversized gene, MYO7A. | Q37710671 | ||
| Clinical applications of retinal gene therapy. | Q38045154 | ||
| AAV-mediated tyrosinase gene transfer restores melanogenesis and retinal function in a model of oculo-cutaneous albinism type I (OCA1). | Q39510173 | ||
| Efficient gene delivery to the cone-enriched pig retina by dual AAV vectors | Q42235082 | ||
| Expanding AAV packaging capacity with trans-splicing or overlapping vectors: a quantitative comparison | Q45880308 | ||
| P407 | language of work or name | English | Q1860 |
| P921 | main subject | vector-borne disease | Q2083837 |
| P304 | page(s) | 153-175 | |
| P577 | publication date | 2018-01-01 | |
| P1433 | published in | Methods in Molecular Biology | Q15752859 |
| P1476 | title | Dual AAV Vectors for Stargardt Disease | |
| P478 | volume | 1715 |
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