| scholarly article | Q13442814 |
| P356 | DOI | 10.1007/S10198-016-0787-0 |
| P8608 | Fatcat ID | release_4t7mxn4ve5aqvjz2ffdayzpqgq |
| P698 | PubMed publication ID | 27062257 |
| P50 | author | Arrigo Schieppati | Q114428691 |
| Domenica Taruscio | Q40018543 | ||
| Juan Oliva-Moreno | Q50795279 | ||
| Imre Boncz | Q52984388 | ||
| Renata Linertová | Q58390326 | ||
| P2093 | author name string | Pedro Serrano-Aguilar | |
| Márta Péntek | |||
| Petra Baji | |||
| Valentin Brodszky | |||
| László Gulácsi | |||
| Ulf Persson | |||
| Panos Kanavos | |||
| Georgi Iskrov | |||
| Karine Chevreul | |||
| Giovanni Fattore | |||
| BURQOL-RD Research Network | |||
| Gábor Pogány | |||
| Julio López-Bastida | |||
| Manuel Posada-de-la-Paz | |||
| Johann Matthias Graf von der Schulenburg | |||
| P2860 | cites work | FUNCTIONAL EVALUATION: THE BARTHEL INDEX | Q28201591 |
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| Diagnosis, quality of life, and treatment of patients with Hunter syndrome in the French healthcare system: a retrospective observational study | Q35532055 | ||
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| Economic valuation of informal care. An overview of methods and applications. | Q35903595 | ||
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| Prevalence rates of mucopolysaccharidoses in Poland | Q40022382 | ||
| Costs and health-related quality of life of patients with cystic fibrosis and their carers in France | Q41528123 | ||
| Cystic fibrosis -- disease burden and health-related quality of life of patients and their caregivers: results of the European BURQOL-RD survey in Hungary | Q45209197 | ||
| Delphi approach to select rare diseases for a European representative survey. The BURQOL-RD study | Q45881556 | ||
| [Health-related quality of life of the Hungarian population]. | Q53809764 | ||
| Expensive drugs for rare disorders: to treat or not to treat? The case of enzyme replacement therapy for mucopolysaccharidosis VI | Q64043856 | ||
| [Shift of focus in the financing of Hungarian drugs. Reimbursement for orphan drugs for treating rare diseases: financing of enzyme replacement therapy in Hungary] | Q64049869 | ||
| Cost-of-illness methodology: a guide to current practices and procedures | Q71960493 | ||
| P304 | page(s) | 89-98 | |
| P577 | publication date | 2016-04-09 | |
| P1433 | published in | The European Journal of Health Economics | Q24883230 |
| P1476 | title | Social/economic costs and health-related quality of life of mucopolysaccharidosis patients and their caregivers in Europe | |
| P478 | volume | 17 Suppl 1 |
| Q93189662 | An online survey of burden of illness in families with mucopolysaccharidosis type II children in the United States |
| Q64250400 | An online survey on burden of illness among families with post-stem cell transplant mucopolysaccharidosis type I children in the United States |
| Q91735364 | Analysis of the caregiver burden associated with Sanfilippo syndrome type B: panel recommendations based on qualitative and quantitative data |
| Q92049089 | Assessing the impact of the five senses on quality of life in mucopolysaccharidoses |
| Q92139201 | Cost-of-illness studies in nine Central and Eastern European countries |
| Q91977557 | Healthcare Resource Utilization and the Cost of Care for Mucopolysaccharidosis I Patients in Iran |
| Q59806220 | Patient and observer reported outcome measures to evaluate health-related quality of life in inherited metabolic diseases: a scoping review |
| Q47787703 | Social/economic costs and health-related quality of life in patients with rare diseases in Europe. |
| Q64904367 | The burden of informal caregiving in Hungary, Poland and Slovenia: results from national representative surveys. |
| Q99362534 | Therapy development for the mucopolysaccharidoses: Updated consensus recommendations for neuropsychological endpoints |
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