Phase 3 Study of Ataluren in Patients With Nonsense Mutation Duchenne Muscular Dystrophy

clinical trial

Phase 3 Study of Ataluren in Patients With Nonsense Mutation Duchenne Muscular Dystrophy is …
instance of (P31):
clinical trialQ30612

External links are
P3098ClinicalTrials.gov IDNCT01826487

P6099clinical trial phasephase III clinical trialQ42824827
P17countryCanadaQ16
SpainQ29
United States of AmericaQ30
BelgiumQ31
SwedenQ34
PolandQ36
ItalyQ38
SwitzerlandQ39
TurkeyQ43
FranceQ142
United KingdomQ145
BrazilQ155
GermanyQ183
ChileQ298
IsraelQ801
AustraliaQ408
P582end time2015-08-01
P921main subjectatalurenQ753330
Becker muscular dystrophyQ2484592
P4135maximum age16
P2899minimum age7
P1132number of participants230
P6153research siteHarvard UniversityQ13371
Columbia UniversityQ49088
University of California, Los AngelesQ174710
University of MinnesotaQ238101
Oregon Health & Science UniversityQ282097
Medical University of WarsawQ496351
Katholieke Universiteit LeuvenQ833670
Rush University Medical CenterQ1535116
Alberta Children's HospitalQ2831698
Children's Hospital of Eastern OntarioQ2945735
Seoul National University HospitalQ4403855
UPMC Children's Hospital of PittsburghQ5098130
Cincinnati Children's Hospital Medical CenterQ5120231
Royal Manchester Children's HospitalQ7374441
University Hospital BrnoQ11989315
Hadassah University Hospital, Mt. ScopusQ16129695
University of Iowa Health CareQ30254145
University of Kansas Medical CenterQ33526980
University of Utah Health CareQ56582915
Hospital Sant Joan de DéuQ64442914
P1813short nameACT DMD
P580start time2013-03-01
P8363study typeinterventional studyQ78089383
P1476titleA Phase 3 Efficacy and Safety Study of Ataluren (PTC124) in Patients With Nonsense Mutation Dystrophinopathy