Stem cell transplantation for the Wiskott-Aldrich syndrome: a single-center experience confirms efficacy of matched unrelated donor transplantation

scientific article published on 02 October 2006

Stem cell transplantation for the Wiskott-Aldrich syndrome: a single-center experience confirms efficacy of matched unrelated donor transplantation is …
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scholarly articleQ13442814

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P6179Dimensions Publication ID1041417337
P356DOI10.1038/SJ.BMT.1705512
P8608Fatcat IDrelease_hmswiulzwreqjgj7zrmhv6axti
P698PubMed publication ID17013426

P2093author name stringLanfranchi A
Mazza C
Imberti L
Giliani S
Notarangelo LD
Porta F
Mazzolari E
Pai SY
Cavagnini S
DeMartiis D
Forino C
Moratto D
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Defects in T-cell-mediated immunity to influenza virus in murine Wiskott-Aldrich syndrome are corrected by oncoretroviral vector-mediated gene transfer into repopulating hematopoietic cellsQ33348939
An international study examining therapeutic options used in treatment of Wiskott-Aldrich syndromeQ33358369
Mutations of the Wiskott-Aldrich Syndrome Protein (WASP): hotspots, effect on transcription, and translation and phenotype/genotype correlationQ33361928
Bone marrow transplantation in 26 patients with Wiskott-Aldrich syndrome from a single centerQ33496652
Defective actin polymerization in EBV-transformed B-cell lines from patients with the Wiskott-Aldrich syndromeQ33503405
Lentiviral vector-mediated gene transfer in T cells from Wiskott-Aldrich syndrome patients leads to functional correction.Q34552235
Lentiviral vectors transcriptionally targeted to hematopoietic cells by WASP gene proximal promoter sequences.Q40449872
Complete Correction of the Wiskott-Aldrich Syndrome by Allogeneic Bone-Marrow TransplantationQ40882151
Impaired thymic output and restricted T-cell repertoire in two infants with immunodeficiency and early-onset generalized dermatitis.Q42695173
Umbilical cord blood transplantation in Wiskott Aldrich syndromeQ43996039
Gene therapy for Wiskott-Aldrich syndrome: rescue of T-cell signaling and amelioration of colitis upon transplantation of retrovirally transduced hematopoietic stem cells in miceQ45856422
Efficacy of gene therapy for Wiskott-Aldrich syndrome using a WAS promoter/cDNA-containing lentiviral vector and nonlethal irradiation.Q45856827
Functional correction of T cells derived from patients with the Wiskott–Aldrich syndrome (WAS) by transduction with an oncoretroviral vector encoding the WAS proteinQ45861740
A lentiviral vector encoding the human Wiskott-Aldrich syndrome protein corrects immune and cytoskeletal defects in WASP knockout mice.Q45880227
Mixed chimera status of 12 patients with Wiskott-Aldrich syndrome (WAS) after hematopoietic stem cell transplantation: evaluation by flow cytometric analysis of intracellular WAS protein expressionQ45888194
Wiskott-Aldrich syndrome protein-deficient mice reveal a role for WASP in T but not B cell activationQ47713209
Marrow transplantation from human leukocyte antigen-identical or haploidentical donors for correction of Wiskott-Aldrich syndrome.Q54283092
Hematopoietic stem cell transplantation in Omenn syndrome: a single-center experienceQ57131881
Clinical manifestations of graft-versus-host disease in human recipients of marrow from HL-A-matched sibling donorsQ70051817
Impact of donor type on outcome of bone marrow transplantation for Wiskott-Aldrich syndrome: collaborative study of the International Bone Marrow Transplant Registry and the National Marrow Donor ProgramQ73586024
Differential contribution of Wiskott-Aldrich syndrome protein to selective advantage in T- and B-cell lineagesQ79077280
P433issue10
P921main subjectWiskott-Aldrich syndromeQ953638
stem cell transplantationQ65592366
P304page(s)671-679
P577publication date2006-10-02
P1433published inBone Marrow TransplantationQ4941523
P1476titleStem cell transplantation for the Wiskott-Aldrich syndrome: a single-center experience confirms efficacy of matched unrelated donor transplantation
P478volume38