| P2093 | author name string | L Zhang | |
| | X Y Dai | |
| P2860 | cites work | Hepatic gene transfer as a means of tolerance induction to transgene products | Q33775537 |
| | Factor IX ectopically expressed in platelets can be stored in alpha-granules and corrects the phenotype of hemophilia B mice | Q34122653 |
| | Long-term safety and efficacy of factor IX gene therapy in hemophilia B. | Q34783922 |
| | Adeno-associated virus antibody profiles in newborns, children, and adolescents | Q35191112 |
| | Adenovirus-associated virus vector-mediated gene transfer in hemophilia B | Q35691659 |
| | Factor IX expression in skeletal muscle of a severe hemophilia B patient 10 years after AAV-mediated gene transfer | Q35876970 |
| | CRISPR/Cas9-mediated somatic correction of a novel coagulator factor IX gene mutation ameliorates hemophilia in mouse | Q37446641 |
| | Novel factor VIII variants with a modified furin cleavage site improve the efficacy of gene therapy for hemophilia A. | Q37614115 |
| | Platelet gene therapy by lentiviral gene delivery to hematopoietic stem cells restores hemostasis and induces humoral immune tolerance in FIX(null) mice | Q37690441 |
| | Recurrent AAV2-related insertional mutagenesis in human hepatocellular carcinomas | Q40613665 |
| | Oral gene therapy for hemophilia B using chitosan-formulated FIX mutants | Q42228305 |
| | The prevalence of neutralizing antibodies against adeno-associated virus capsids is reduced in young Japanese individuals | Q42261520 |
| | The incidence of factor VIII inhibitors in severe haemophilia A following a major switch from full-length to B-domain-deleted factor VIII: a prospective cohort comparison | Q45870049 |
| | Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant. | Q45875499 |
| | Permanent partial phenotypic correction and tolerance in a mouse model of hemophilia B by stem cell gene delivery of human factor IX. | Q45886876 |
| P433 | issue | 4 | |
| P921 | main subject | hemophilia | Q134003 |
| P1104 | number of pages | 3 | |
| P304 | page(s) | 350-352 | |
| P577 | publication date | 2018-04-01 | |
| P1433 | published in | Chinese Journal of Hematology | Q27714364 |
| P1476 | title | [Research advances on gene therapy for hemophilia] | |
| P478 | volume | 39 | |