| scholarly article | Q13442814 |
| P50 | author | Kay Davies | Q6380176 |
| P2093 | author name string | Simon Guiraud | |
| P2860 | cites work | Very mild muscular dystrophy associated with the deletion of 46% of dystrophin | Q34371637 |
| Adeno-associated viral (AAV) vectors do not efficiently target muscle satellite cells | Q34886209 | ||
| Adeno-associated virus vector carrying human minidystrophin genes effectively ameliorates muscular dystrophy in mdx mouse model | Q35573761 | ||
| Dystrophins carrying spectrin-like repeats 16 and 17 anchor nNOS to the sarcolemma and enhance exercise performance in a mouse model of muscular dystrophy. | Q37111368 | ||
| The Pathogenesis and Therapy of Muscular Dystrophies | Q38517557 | ||
| Progress toward Gene Therapy for Duchenne Muscular Dystrophy | Q39246797 | ||
| Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy. | Q40109350 | ||
| Human dystrophin expression corrects the myopathic phenotype in transgenic mdx mice | Q45716447 | ||
| Differential effects of dystrophin and utrophin gene transfer in immunocompetent muscular dystrophy (mdx) mice | Q45871277 | ||
| Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy | Q45883916 | ||
| Cardiac specific expression of ∆H2-R15 mini-dystrophin normalized all ECG abnormalities and the end-diastolic volume in a 23-m-old mouse model of Duchenne dilated cardiomyopathy. | Q50058440 | ||
| Dystrophin's central domain forms a complex filament that becomes disorganized by in-frame deletions. | Q52357025 | ||
| Systemic AAV Micro-dystrophin Gene Therapy for Duchenne Muscular Dystrophy | Q57039821 | ||
| Codon and mRNA Sequence Optimization of Microdystrophin Transgenes Improves Expression and Physiological Outcome in Dystrophic mdx Mice Following AAV2/8 Gene Transfer | Q61718084 | ||
| Diaphragm rescue alone prevents heart dysfunction in dystrophic mice | Q82381994 | ||
| Development of Novel Micro-dystrophins with Enhanced Functionality | Q91338916 | ||
| P433 | issue | 3 | |
| P921 | main subject | Duchenne muscular dystrophy | Q1648484 |
| P304 | page(s) | 486-488 | |
| P577 | publication date | 2019-02-12 | |
| P1433 | published in | Molecular Therapy | Q15762400 |
| P1476 | title | Micro-dystrophin Genes Bring Hope of an Effective Therapy for Duchenne Muscular Dystrophy | |
| P478 | volume | 27 |
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