scholarly article | Q13442814 |
P2093 | author name string | Fabienne Rajas | |
Gilles Mithieux | |||
Hye-Ri Kang | |||
Charles P Venditti | |||
Randy J Chandler | |||
Dwight D Koeberl | |||
Songtao Li | |||
Shawn M Burgess | |||
Elizabeth D Brooks | |||
Zelin Chen | |||
Monika Gjorgjieva | |||
Lauren R Waskowicz | |||
Kylie M Grady | |||
Stephanie N Smith | |||
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Long-term efficacy following readministration of an adeno-associated virus vector in dogs with glycogen storage disease type Ia | Q33720634 | ||
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Prevention of hepatocellular adenoma and correction of metabolic abnormalities in murine glycogen storage disease type Ia by gene therapy | Q36336550 | ||
Genotoxicity in Mice Following AAV Gene Delivery: A Safety Concern for Human Gene Therapy? | Q36756903 | ||
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Hepatic glucose-6-phosphatase-α deficiency leads to metabolic reprogramming in glycogen storage disease type Ia. | Q52726308 | ||
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Resection of hepatocellular adenoma in patients with glycogen storage disease type Ia | Q80631871 | ||
Targeted deletion of liver glucose-6 phosphatase mimics glycogen storage disease type 1a including development of multiple adenomas | Q82615010 | ||
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Long-term safety and efficacy of AAV gene therapy in the canine model of glycogen storage disease type Ia | Q88868479 | ||
Long-term complications of glycogen storage disease type Ia in the canine model treated with gene replacement therapy | Q90457188 | ||
Dietary exacerbation of metabolic stress leads to accelerated hepatic carcinogenesis in glycogen storage disease type Ia | Q91334741 | ||
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Bezafibrate induces autophagy and improves hepatic lipid metabolism in glycogen storage disease type Ia | Q91765348 | ||
P921 | main subject | glycogen storage disease | Q1421738 |
P1104 | number of pages | 9 | |
P304 | page(s) | 383-391 | |
P577 | publication date | 2019-11-11 | |
P1433 | published in | Molecular Therapy. Methods & Clinical Development | Q27725341 |
P1476 | title | Pathogenesis of Hepatic Tumors following Gene Therapy in Murine and Canine Models of Glycogen Storage Disease | |
P478 | volume | 15 |
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