review article | Q7318358 |
scholarly article | Q13442814 |
P6179 | Dimensions Publication ID | 1012856377 |
P356 | DOI | 10.1023/A:1022548232735 |
P698 | PubMed publication ID | 10227692 |
P2093 | author name string | Barranger JA | |
Swaney WP | |||
Rice EO | |||
P2860 | cites work | Cloning and expression of human arylsulfatase A | Q24316271 |
Proteoglycan-collagen arrangements in developing rat tail tendon. An electron microscopical and biochemical investigation | Q24530776 | ||
Adeno-associated virus (AAV) Rep proteins mediate complex formation between AAV DNA and its integration site in human DNA | Q24562760 | ||
Cytological evidence for a relationship between normal hemotopoietic colony-forming cells and cells of the lymphoid system | Q24679408 | ||
Second-strand synthesis is a rate-limiting step for efficient transduction by recombinant adeno-associated virus vectors | Q24682739 | ||
Transduction with recombinant adeno-associated virus for gene therapy is limited by leading-strand synthesis | Q24684374 | ||
Single-Step Method of RNA Isolation by Acid Guanidinium Thiocyanate–Phenol–Chloroform Extraction | Q25938986 | ||
Reversal of pathology in murine mucopolysaccharidosis type VII by somatic cell gene transfer | Q28115950 | ||
Molecular basis of different forms of metachromatic leukodystrophy | Q28240698 | ||
Structure of the arylsulfatase A gene | Q28258513 | ||
Multipotent neural cell lines can engraft and participate in development of mouse cerebellum | Q28290006 | ||
Amphetamine-induced behavioral phenotype in a hypoxanthine-guanine phosphoribosyltransferase-deficient mouse model of Lesch-Nyhan syndrome | Q28589709 | ||
Phenotype of arylsulfatase A-deficient mice: relationship to human metachromatic leukodystrophy | Q30530571 | ||
Stromal support enhances cell-free retroviral vector transduction of human bone marrow long-term culture-initiating cells | Q30841597 | ||
Tracing transplanted oligodendrocytes during migration and maturation in the shiverer mouse brain | Q33268443 | ||
A further example of human blood group chimaerism | Q33587717 | ||
Safe and efficient generation of recombinant retroviruses with amphotropic and ecotropic host ranges | Q33644899 | ||
Correction of murine mucopolysaccharidosis type VII (MPS VII) by bone marrow transplantation and gene transfer therapy | Q68000936 | ||
Lysosomal enzyme replacement in neural tissue by allogeneic bone marrow transplantation following total lymphoid irradiation in canine fucosidosis | Q68940330 | ||
Infantile (type II) Gaucher's disease: in utero diagnosis and fetal pathology | Q69454868 | ||
Histological improvement and enzyme replacement in the brains of fucosidosis dogs after bone marrow engraftment | Q69494732 | ||
CNS neuronal cell line-derived factors regulate gliogenesis in neonatal rat brain cultures | Q69849076 | ||
A quantitative immunohistochemical study of macroglial cell development in the rat optic nerve: in vivo evidence for two distinct astrocyte lineages | Q69904315 | ||
Ontogeny of human hematopoietic cells: analysis utilizing monoclonal antibodies | Q70149544 | ||
Myelin formation following transplantation of normal fetal glia into myelin-deficient rat spinal cord | Q70245805 | ||
Long-term neurological effects of bone marrow transplantation in a canine lysosomal storage disease | Q70416914 | ||
Sulfatides in prenatal metachromatic leukodystrophy | Q71106507 | ||
Gene transfer into hematopoietic cells. Implications for cancer therapy | Q71632094 | ||
Growth factors and stromal support generate very efficient retroviral transduction of peripheral blood CD34+ cells from Gaucher patients | Q71698782 | ||
Transduction, expression, and secretion of human glucocerebrosidase by murine myoblasts | Q72043646 | ||
Retroviral vector design for long-term expression in murine hematopoietic cells in vivo | Q72175909 | ||
Male donor-derived cells in the brains of female sex-mismatched bone marrow transplant recipients: a Y-chromosome specific in situ hybridization study | Q72230155 | ||
Correction of enzyme deficiency in metachromatic leukodystrophy fibroblasts by retroviral-mediated transfer of the human arylsulphatase A gene | Q72665523 | ||
Myelination by cryopreserved xenografts and allografts in the myelin-deficient rat | Q72787100 | ||
Presymptomatic late-infantile metachromatic leukodystrophy treated with bone marrow transplantation | Q72817537 | ||
Molecular genetics of metachromatic leukodystrophy | Q72823011 | ||
Increased titer of recombinant AAV vectors by gene transfer with adenovirus coupled to DNA-polylysine complexes | Q45867335 | ||
Cells expressing human glucocerebrosidase from a retroviral vector repopulate macrophages and central nervous system microglia after murine bone marrow transplantation | Q45872830 | ||
Retroviral gene transfer and sustained expression of human arylsulfatase A. | Q45877658 | ||
Antisense inhibition and adeno-associated viral vector delivery for reducing hypertension | Q45880713 | ||
Retroviral vector-mediated transfer of the bacterial neomycin resistance gene into fetal and adult sheep and human hematopoietic progenitors in vitro | Q45883579 | ||
Analysis of optimal conditions for retroviral-mediated transduction of primitive human hematopoietic cells | Q46841447 | ||
Structure of the mouse arylsulfatase A gene and cDNA. | Q48085754 | ||
Transplantation of fetal substantia nigra and adrenal medulla to the caudate nucleus in two patients with Parkinson's disease | Q48124004 | ||
Transplantation of oligodendrocytes in the newborn mouse brain: extension of myelination by transplanted cells. Anatomical study | Q48207621 | ||
Disappearance of lysosomal storage in spleen and liver of mucopolysaccharidosis VII mice after transplantation of genetically modified bone marrow cells. | Q48232780 | ||
Transplantation of human embryonic oligodendrocytes into shiverer brain | Q48248251 | ||
Treatment of murine mucopolysaccharidosis type VII by syngeneic bone marrow transplantation in neonates | Q48269245 | ||
Long-term outcome of Hurler syndrome following bone marrow transplantation | Q48303127 | ||
Stimulation of oligodendroglial proliferation and maturation by interleukin-2. | Q48334072 | ||
Transplantations of newborn CNS fragments into the brain of shiverer mutant mice: extensive myelination by transplanted oligodendrocytes. II. Electron microscopic study | Q48391947 | ||
Transplantation of fetal dopamine neurons in Parkinson's disease: PET [18F]6-L-fluorodopa studies in two patients with putaminal implants | Q48535750 | ||
Ultrastructural studies of eight cases of fetal Tay-Sachs disease | Q48605176 | ||
Increased life span and correction of metabolic defects in murine mucopolysaccharidosis type VII after syngeneic bone marrow transplantation. | Q48612902 | ||
Delivery of active hexosaminidase across the blood-brain barrier in rats | Q48640985 | ||
Fetal homotransplants (ventral mesencephalon and adrenal tissue) to the striatum of parkinsonian subjects | Q48848737 | ||
A brain transplant that works | Q48968411 | ||
Insulin-like growth factor I promotes cell proliferation and oligodendroglial commitment in rat glial progenitor cells developing in vitro. | Q51185222 | ||
Bone-marrow transplantation for metachromatic leucodystrophy. | Q52265930 | ||
Chimerism following fetal transfusion. Report of leucocyte hybridization and infant with acute lymphocytic leukaemia. | Q54168796 | ||
Bone Marrow and Lymphoid Cell Injection of the Pig Foetus resulting in Transplantation Tolerance or Immunity and Immunoglobulin Production | Q59017328 | ||
Ovarian teratomas in mice are derived from oocytes that have completed the first meiotic division | Q59053402 | ||
Repair of demyelinated lesions by transplantation of purified 0-2A progenitor cells | Q59079119 | ||
Platelet-derived growth factor promotes division and motility and inhibits premature differentiation of the oligodendrocyte/type-2 astrocyte progenitor ceil | Q59093382 | ||
Neural transplantation in Parkinson's disease: the Swedish experience | Q59575149 | ||
Treatment of Late Infantile Metachromatic Leukodystrophy by Bone Marrow Transplantation | Q61769085 | ||
Bone marrow transplantation for Sanfilippo disease type B | Q67476865 | ||
Cytokine stimulation of multilineage hematopoiesis from immature human cells engrafted in SCID mice | Q67532844 | ||
SCID-hu mice as a model to study tolerance after fetal stem cell transplantation | Q67884354 | ||
Cooperation between two growth factors promotes extended self-renewal and inhibits differentiation of oligodendrocyte-type-2 astrocyte (O-2A) progenitor cells | Q33751730 | ||
Perivascular microglial cells of the CNS are bone marrow-derived and present antigen in vivo | Q34049368 | ||
Bone marrow transplantation in canine mucopolysaccharidosis I. Effects within the central nervous system | Q34165972 | ||
Behavioral consequences of bone marrow transplantation in the treatment of murine mucopolysaccharidosis type VII. | Q34185051 | ||
FGF modulates the PDGF-driven pathway of oligodendrocyte development. | Q34196379 | ||
Actively acquired tolerance of foreign cells | Q34233179 | ||
Correction of lysosomal storage in the liver and spleen of MPS VII mice by implantation of genetically modified skin fibroblasts | Q34352418 | ||
Bone marrow transplantation corrects the enzyme defect in neurons of the central nervous system in a lysosomal storage disease | Q35147265 | ||
Gaucher disease in the neonate: a distinct Gaucher phenotype is analogous to a mouse model created by targeted disruption of the glucocerebrosidase gene | Q35530647 | ||
Bone marrow transplantation in the treatment of alpha-mannosidosis | Q35604213 | ||
Asymmetric replication in vitro from a human sequence element is dependent on adeno-associated virus Rep protein | Q35837075 | ||
Determination of adeno-associated virus Rep68 and Rep78 binding sites by random sequence oligonucleotide selection | Q35851511 | ||
Analysis of recombinant adeno-associated virus packaging and requirements for rep and cap gene products | Q35877884 | ||
Transplantation of an oligodendrocyte cell line leading to extensive myelination | Q35926039 | ||
Pluripotential hemopoietic stem cells in adult mouse brain | Q36292982 | ||
Transplanted transgenically marked oligodendrocytes survive, migrate and myelinate in the normal mouse brain as they do in the shiverer mouse brain | Q36738960 | ||
Redesign of retrovirus packaging cell lines to avoid recombination leading to helper virus production | Q36918698 | ||
Regulated high level expression of a human gamma-globin gene introduced into erythroid cells by an adeno-associated virus vector | Q37142195 | ||
Efficient transfer and sustained high expression of the human glucocerebrosidase gene in mice and their functional macrophages following transplantation of bone marrow transduced by a retroviral vector | Q37319132 | ||
Recombinant junctions formed by site-specific integration of adeno-associated virus into an episome | Q38290022 | ||
Fetal Metachromatic Leukodystrophy: Pathology, Biochemistry and a Study of In Vitro Enzyme Replacement in CNS Tissue | Q39122613 | ||
Grafts of fetal dopamine neurons survive and improve motor function in Parkinson's disease | Q39519102 | ||
Long-term follow-up of a patient transplanted for Hunter's disease type IIB: a case report and literature review. | Q40594641 | ||
Quantitative aspects of fetal liver cell transplantation in animals and man | Q40635416 | ||
The O-2A lineage: from rats to humans | Q40681589 | ||
Fetal liver transplantation: biology and clinical results | Q40883758 | ||
Expansion of rat oligodendrocyte progenitors into proliferative "oligospheres" that retain differentiation potential | Q41170983 | ||
High-efficiency transfer of the T cell co-stimulatory molecule B7-2 to lymphoid cells using high-titer recombinant adeno-associated virus vectors | Q41263327 | ||
Efficient retroviral mediated transfer of the glucocerebrosidase gene in CD34+ enriched umbilical cord blood human hematopoietic progenitors | Q41265431 | ||
Cell lines for the production of recombinant adeno-associated virus | Q41286219 | ||
Centrifugal enhancement of retroviral mediated gene transfer | Q41315284 | ||
Neural progenitor cell engraftment corrects lysosomal storage throughout the MPS VII mouse brain | Q41358776 | ||
Retroviral stem cell gene therapy | Q41487206 | ||
Quantitative correlation between the residual activity of beta-hexosaminidase A and arylsulfatase A and the severity of the resulting lysosomal storage disease | Q41638167 | ||
CG-4, a new bipotential glial cell line from rat brain, is capable of differentiating in vitro into either mature oligodendrocytes or type-2 astrocytes | Q41645595 | ||
Determination of the origin and nature of brain macrophages and microglial cells in mouse central nervous system, using non-radioactive in situ hybridization and immunoperoxidase techniques | Q41652011 | ||
Type 2 and type 3 Gaucher disease: a morphological and biochemical study | Q42221976 | ||
Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain | Q42280576 | ||
Myelination by oligodendrocytes isolated from 4-6-week-old rat central nervous system and transplanted into newborn shiverer brain | Q42489809 | ||
Extracellular matrix-associated molecules collaborate with ciliary neurotrophic factor to induce type-2 astrocyte development | Q42762723 | ||
Long-term survival of grafted cells, dopamine synthesis/release, synaptic connections, and functional recovery after transplantation of fetal nigral cells in rats with unilateral 6-OHDA lesions in the nigrostriatal dopamine pathway | Q44049498 | ||
Transplantation of fetal dopamine neurons in Parkinson's disease: one-year clinical and neurophysiological observations in two patients with putaminal implants | Q44132651 | ||
Human fetal dopamine neurons grafted into the striatum in two patients with severe Parkinson's disease. A detailed account of methodology and a 6-month follow-up | Q44995599 | ||
Efficient retroviral gene transfer to purified long-term repopulating hematopoietic stem cells | Q45098814 | ||
Differentiation of a bipotential glial progenitor cell in a single cell microculture | Q45248944 | ||
High-level globin gene expression mediated by a recombinant adeno-associated virus genome that contains the 3' gamma globin gene regulatory element and integrates as tandem copies in erythroid cells | Q45764380 | ||
Expression of the human glucocerebrosidase and arylsulfatase A genes in murine and patient primary fibroblasts transduced by an adeno-associated virus vector | Q45788473 | ||
P433 | issue | 4 | |
P304 | page(s) | 601-615 | |
P577 | publication date | 1999-04-01 | |
P1433 | published in | Neurochemical Research | Q15716728 |
P1476 | title | Gene transfer approaches to the lysosomal storage disorders | |
P478 | volume | 24 |
Q42817051 | Absence of metabolic cross-correction in Tay-Sachs cells: implications for gene therapy |
Q48522524 | Apparent diffusion coefficient vale of the brain in patients with Gaucher's disease type II and type III. |
Q34261291 | Clinical gene therapy in hematology: past and future |
Q34188392 | Current developments in the design of onco-retrovirus and lentivirus vector systems for hematopoietic cell gene therapy |
Q34224260 | From gene transfer to gene therapy in lysosomal storage diseases affecting the central nervous system |
Q34941895 | Glycosphingolipid lysosomal storage diseases: therapy and pathogenesis |
Q35158023 | Hematopoietic stem cell gene therapy: progress toward therapeutic targets |
Q40740222 | High efficiency lentiviral gene delivery in non-dividing cells by deoxynucleoside treatment |
Q34238653 | Positional candidate gene cloning of CLN1. |
Q34471626 | Remaining problems in the management of patients with Gaucher disease |
Q44858665 | Restoration of the GM2 ganglioside metabolism in bone marrow-derived stromal cells from Tay-Sachs disease animal model |
Q74101103 | [Treatment of type 1 Gaucher's disease. Still a long way to go] |