| scholarly article | Q13442814 |
| P50 | author | Federico Mingozzi | Q89436980 |
| P2093 | author name string | Katherine A High | |
| Valder R Arruda | |||
| Bernd Hauck | |||
| J Fraser Wright | |||
| Patricia Favaro | |||
| Harre D Downey | |||
| J Shangzhen Zhou | |||
| P2860 | cites work | Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions | Q24531466 |
| Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy | Q24535690 | ||
| Safety and efficacy of gene transfer for Leber's congenital amaurosis | Q24634724 | ||
| Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response | Q29619095 | ||
| Immune responses to adenovirus and adeno-associated virus in humans. | Q33874473 | ||
| AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B. | Q34168942 | ||
| Identification of PDGFR as a receptor for AAV-5 transduction | Q34264144 | ||
| Adeno-associated virus vectors can be efficiently produced without helper virus | Q34479933 | ||
| Human fibroblast growth factor receptor 1 is a co-receptor for infection by adeno-associated virus 2. | Q34486856 | ||
| AlphaVbeta5 integrin: a co-receptor for adeno-associated virus type 2 infection | Q34486863 | ||
| Induction of immune tolerance to coagulation factor IX antigen by in vivo hepatic gene transfer | Q34985105 | ||
| The 37/67-kilodalton laminin receptor is a receptor for adeno-associated virus serotypes 8, 2, 3, and 9 | Q35101411 | ||
| Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman primate liver | Q35848563 | ||
| Modulation of tolerance to the transgene product in a nonhuman primate model of AAV-mediated gene transfer to liver. | Q36007714 | ||
| Phase 1 trial of FVIII gene transfer for severe hemophilia A using a retroviral construct administered by peripheral intravenous infusion | Q38520320 | ||
| Gene therapy vectors based on adeno-associated virus type 1. | Q39550492 | ||
| Epitope mapping of human anti-adeno-associated virus type 2 neutralizing antibodies: implications for gene therapy and virus structure | Q39589248 | ||
| Comparison of the ability of adeno-associated viral vectors pseudotyped with serotype 2, 5, and 8 capsid proteins to mediate efficient transduction of the liver in murine and nonhuman primate models | Q40418515 | ||
| Quantification of adeno-associated virus particles and empty capsids by optical density measurement | Q40672137 | ||
| Generation and characterization of chimeric recombinant AAV vectors | Q41869331 | ||
| Effects of transient immunosuppression on adenoassociated, virus-mediated, liver-directed gene transfer in rhesus macaques and implications for human gene therapy | Q41999615 | ||
| Therapeutic levels of functional human factor X in rats after retroviral-mediated hepatic gene therapy. | Q42803722 | ||
| Factor IX variants improve gene therapy efficacy for hemophilia B. | Q43527094 | ||
| Human immunoglobulin inhibits liver transduction by AAV vectors at low AAV2 neutralizing titers in SCID mice | Q43847196 | ||
| Inadvertent germline transmission of AAV2 vector: findings in a rabbit model correlate with those in a human clinical trial | Q44328165 | ||
| CD8(+) T-cell responses to adeno-associated virus capsid in humans | Q45406111 | ||
| Phase I trial of intramuscular injection of a recombinant adeno-associated virus serotype 2 alphal-antitrypsin (AAT) vector in AAT-deficient adults | Q45409947 | ||
| Sustained high-level expression of human factor IX (hFIX) after liver-targeted delivery of recombinant adeno-associated virus encoding the hFIX gene in rhesus macaques | Q45731350 | ||
| A seroepidemiologic study of adenovirus-associated virus infection in infants and children | Q45821424 | ||
| Multiyear therapeutic benefit of AAV serotypes 2, 6, and 8 delivering factor VIII to hemophilia A mice and dogs | Q45856596 | ||
| The rhesus macaque as an animal model for hemophilia B gene therapy | Q45856806 | ||
| Evidence of multiyear factor IX expression by AAV-mediated gene transfer to skeletal muscle in an individual with severe hemophilia B. | Q45859498 | ||
| Analysis of testes and semen from rabbits treated by intravenous injection with a retroviral vector encoding the human factor VIII gene: no evidence of germ line transduction | Q45873156 | ||
| Lack of germline transmission of vector sequences following systemic administration of recombinant AAV-2 vector in males | Q45881920 | ||
| Identification of factors that contribute to recombinant AAV2 particle aggregation and methods to prevent its occurrence during vector purification and formulation | Q46553714 | ||
| Sustained AAV-mediated dystrophin expression in a canine model of Duchenne muscular dystrophy with a brief course of immunosuppression | Q80141652 | ||
| P433 | issue | 6 | |
| P304 | page(s) | 1022-1030 | |
| P577 | publication date | 2009-03-17 | |
| P1433 | published in | Molecular Therapy | Q15762400 |
| P1476 | title | Host and vector-dependent effects on the risk of germline transmission of AAV vectors | |
| P478 | volume | 17 |
| Q37730113 | Biodistribution of AAV8 vectors expressing human low-density lipoprotein receptor in a mouse model of homozygous familial hypercholesterolemia |
| Q21092431 | Endogenous viral elements in animal genomes |
| Q99579530 | Gene Therapy for Hemophilia: Facts and Quandaries in the 21st Century |
| Q83408160 | Gene-based passive antibody protection from HIV |
| Q99584195 | High-Resolution Histological Landscape of AAV DNA Distribution in Cellular Compartments and Tissues following Local and Systemic Injection |
| Q35568518 | Intranasal administration of adeno-associated virus type 12 (AAV12) leads to transduction of the nasal epithelia and can initiate transgene-specific immune response |
| Q55360441 | In Vivo Genetic Manipulation of Spermatogonial Stem Cells and Their Microenvironment by Adeno-Associated Viruses. |
| Q39553052 | Liver-Directed Adeno-Associated Viral Gene Therapy for Hemophilia |
| Q41347222 | Non-clinical Safety and Efficacy of an AAV2/8 Vector Administered Intravenously for Treatment of Mucopolysaccharidosis Type VI. |
| Q38529941 | Obstacles and future of gene therapy for hemophilia |
| Q61811179 | Preclinical Development of an AAV8-hUGT1A1 Vector for the Treatment of Crigler-Najjar Syndrome |
| Q35101904 | Safety of liver gene transfer following peripheral intravascular delivery of adeno-associated virus (AAV)-5 and AAV-6 in a large animal model |
| Q30644848 | Sustained normalization of neurological disease after intracranial gene therapy in a feline model |
| Q26823818 | The gene therapy journey for hemophilia: are we there yet? |
| Q37866086 | Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challenges |
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