| P2093 | author name string | Katherine A High | |
| | Valder R Arruda | |
| | J Fraser Wright | |
| | Jonathan D Finn | |
| | Joshua I Siner | |
| | Patricia Favaro | |
| P2860 | cites work | Mutational analysis of the adeno-associated virus type 2 (AAV2) capsid gene and construction of AAV2 vectors with altered tropism | Q24515072 |
| | Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy | Q24535690 |
| | Treatment of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trial | Q24608049 |
| | Safety and efficacy of gene transfer for Leber's congenital amaurosis | Q24634724 |
| | Self-complementary recombinant adeno-associated virus (scAAV) vectors promote efficient transduction independently of DNA synthesis | Q28213353 |
| | Rapid evolution of a protein in vitro by DNA shuffling | Q28245873 |
| | Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial | Q28262431 |
| | Effect of gene therapy on visual function in Leber's congenital amaurosis | Q28277981 |
| | Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response | Q29619095 |
| | Host and vector-dependent effects on the risk of germline transmission of AAV vectors | Q33713716 |
| | The pleiotropic effects of natural AAV infections on liver-directed gene transfer in macaques | Q33730459 |
| | Epidermal growth factor receptor is a co-receptor for adeno-associated virus serotype 6. | Q33913409 |
| | Peripheral transvenular delivery of adeno-associated viral vectors to skeletal muscle as a novel therapy for hemophilia B. | Q33931862 |
| | AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B. | Q34168942 |
| | Identification of PDGFR as a receptor for AAV-5 transduction | Q34264144 |
| | Rapid and highly efficient transduction by double-stranded adeno-associated virus vectors in vitro and in vivo | Q34277742 |
| | Improved hepatic gene transfer by using an adeno-associated virus serotype 5 vector | Q34348760 |
| | PDGF and the testis | Q34467046 |
| | Adeno-associated virus vectors can be efficiently produced without helper virus | Q34479933 |
| | Analysis of AAV serotypes 1-9 mediated gene expression and tropism in mice after systemic injection | Q34770058 |
| | Prevalence of neutralizing antibodies against adeno-associated virus (AAV) types 2, 5, and 6 in cystic fibrosis and normal populations: Implications for gene therapy using AAV vectors | Q34938807 |
| | Induction of robust immune responses against human immunodeficiency virus is supported by the inherent tropism of adeno-associated virus type 5 for dendritic cells | Q35186003 |
| | Percutaneous transendocardial delivery of self-complementary adeno-associated virus 6 achieves global cardiac gene transfer in canines. | Q35621815 |
| | Safe and efficient transduction of the liver after peripheral vein infusion of self-complementary AAV vector results in stable therapeutic expression of human FIX in nonhuman primates | Q35628868 |
| | Next generation of adeno-associated virus 2 vectors: point mutations in tyrosines lead to high-efficiency transduction at lower doses | Q36685842 |
| | Gene therapy in large animal models of muscular dystrophy | Q37396408 |
| | Adeno-associated virus types 5 and 6 use distinct receptors for cell entry | Q40330670 |
| | Comparison of the ability of adeno-associated viral vectors pseudotyped with serotype 2, 5, and 8 capsid proteins to mediate efficient transduction of the liver in murine and nonhuman primate models | Q40418515 |
| | Quantification of adeno-associated virus particles and empty capsids by optical density measurement | Q40672137 |
| | Inclusion of the hepatic locus control region, an intron, and untranslated region increases and stabilizes hepatic factor IX gene expression in vivo but not in vitro | Q40863120 |
| | Effects of transient immunosuppression on adenoassociated, virus-mediated, liver-directed gene transfer in rhesus macaques and implications for human gene therapy | Q41999615 |
| | Therapeutic levels of functional human factor X in rats after retroviral-mediated hepatic gene therapy. | Q42803722 |
| | Factor IX variants improve gene therapy efficacy for hemophilia B. | Q43527094 |
| | Sustained correction of disease in naive and AAV2-pretreated hemophilia B dogs: AAV2/8-mediated, liver-directed gene therapy | Q43801966 |
| | Human immunoglobulin inhibits liver transduction by AAV vectors at low AAV2 neutralizing titers in SCID mice | Q43847196 |
| | Prevalence of serum IgG and neutralizing factors against adeno-associated virus (AAV) types 1, 2, 5, 6, 8, and 9 in the healthy population: implications for gene therapy using AAV vectors | Q44258968 |
| | Inadvertent germline transmission of AAV2 vector: findings in a rabbit model correlate with those in a human clinical trial | Q44328165 |
| | Preclinical in vivo evaluation of pseudotyped adeno-associated virus vectors for liver gene therapy | Q44976981 |
| | Sustained high-level expression of human factor IX (hFIX) after liver-targeted delivery of recombinant adeno-associated virus encoding the hFIX gene in rhesus macaques | Q45731350 |
| | Multiyear therapeutic benefit of AAV serotypes 2, 6, and 8 delivering factor VIII to hemophilia A mice and dogs | Q45856596 |
| | Evidence of multiyear factor IX expression by AAV-mediated gene transfer to skeletal muscle in an individual with severe hemophilia B. | Q45859498 |
| | Lack of germline transmission of vector sequences following systemic administration of recombinant AAV-2 vector in males | Q45881920 |
| | Worldwide epidemiology of neutralizing antibodies to adeno-associated viruses. | Q45882349 |
| | Biology of AAV serotype vectors in liver-directed gene transfer to nonhuman primates. | Q45887588 |
| | Functional Epidermal Growth Factor Receptor Localizes to the Postacrosomal Region of Human Spermatozoa | Q63533118 |
| | Localization of the epidermal growth factor (EGF) in the epididymis and accessory genital glands of the boar and functional effects on spermatozoa | Q81728723 |
| P433 | issue | 7 | |
| P407 | language of work or name | English | Q1860 |
| P304 | page(s) | 843-852 | |
| P577 | publication date | 2011-03-08 | |
| P1433 | published in | Human Gene Therapy | Q15757580 |
| P1476 | title | Safety of liver gene transfer following peripheral intravascular delivery of adeno-associated virus (AAV)-5 and AAV-6 in a large animal model | |
| P478 | volume | 22 | |