| P50 | author | Sue Fletcher | Q55590323 |
| | Chalermchai Mitrpant | Q56879268 |
| P2093 | author name string | Francesco Muntoni | |
| | Steve D Wilton | |
| | Abbie M Adams | |
| | Penny L Meloni | |
| P2860 | cites work | Antisense oligonucleotide-induced exon skipping restores dystrophin expression in vitro in a canine model of DMD. | Q45858623 |
| | Maximum entropy modeling of short sequence motifs with applications to RNA splicing signals | Q48531006 |
| | Targeted exon skipping as a potential gene correction therapy for Duchenne muscular dystrophy. | Q52547202 |
| | Antisense oligonucleotide-induced exon skipping across the human dystrophin gene transcript. | Q55043089 |
| | The muscular dystrophies | Q77731754 |
| | Improved antisense oligonucleotide induced exon skipping in the mdx mouse model of muscular dystrophy | Q78537474 |
| | Splicing mosaic of the myophosphorylase gene due to a silent mutation in McArdle disease | Q79324054 |
| | Deletion of exon 16 of the dystrophin gene is not associated with disease | Q79568411 |
| | DMD pseudoexon mutations: splicing efficiency, phenotype, and potential therapy | Q80145954 |
| | Local dystrophin restoration with antisense oligonucleotide PRO051 | Q80412961 |
| | By-passing the nonsense mutation in the 4 CV mouse model of muscular dystrophy by induced exon skipping | Q82591542 |
| | Restoration of correct splicing in thalassemic pre-mRNA by antisense oligonucleotides | Q24561454 |
| | Splicing regulation: from a parts list of regulatory elements to an integrated splicing code | Q24642620 |
| | Antisense oligonucleotide induced exon skipping and the dystrophin gene transcript: cocktails and chemistries | Q27480935 |
| | Mechanisms of alternative pre-messenger RNA splicing | Q28131822 |
| | Comprehensive proteomic analysis of the human spliceosome | Q28201545 |
| | Comparative analysis identifies exonic splicing regulatory sequences--The complex definition of enhancers and silencers | Q28247879 |
| | Pre-mRNA splicing: awash in a sea of proteins | Q29547272 |
| | ESEfinder: A web resource to identify exonic splicing enhancers | Q29616126 |
| | Listening to silence and understanding nonsense: exonic mutations that affect splicing | Q29618493 |
| | Predictive identification of exonic splicing enhancers in human genes | Q29618621 |
| | Transcriptome and genome conservation of alternative splicing events in humans and mice. | Q30753313 |
| | An increased specificity score matrix for the prediction of SF2/ASF-specific exonic splicing enhancers | Q33249150 |
| | Function and genetics of dystrophin and dystrophin-related proteins in muscle | Q34120764 |
| | The architecture of pre-mRNAs affects mechanisms of splice-site pairing. | Q34132523 |
| | The spliceosome: the most complex macromolecular machine in the cell? | Q34278742 |
| | Rules of engagement: co-transcriptional recruitment of pre-mRNA processing factors | Q34419716 |
| | Protein composition of human prespliceosomes isolated by a tobramycin affinity-selection method | Q34429680 |
| | Antisense-induced exon skipping and synthesis of dystrophin in the mdx mouse | Q34582428 |
| | The influence of antisense oligonucleotide length on dystrophin exon skipping. | Q34590393 |
| | Muscular dystrophy into the new millennium | Q34682745 |
| | Induction of revertant fibres in the mdx mouse using antisense oligonucleotides | Q34691050 |
| | How prevalent is functional alternative splicing in the human genome? | Q35640491 |
| | Experience and strategy for the molecular testing of Duchenne muscular dystrophy | Q35789975 |
| | Primary mouse myoblast purification, characterization, and transplantation for cell-mediated gene therapy | Q36534906 |
| | Altered splicing in prelamin A-associated premature aging phenotypes | Q36640178 |
| | Variation in sequence and organization of splicing regulatory elements in vertebrate genes | Q37591781 |
| | Functional analysis of 114 exon-internal AONs for targeted DMD exon skipping: indication for steric hindrance of SR protein binding sites | Q38317038 |
| | Towards a therapeutic inhibition of dystrophin exon 23 splicing in mdx mouse muscle induced by antisense oligoribonucleotides (splicomers): target sequence optimisation using oligonucleotide arrays | Q38336213 |
| | In situ transcription and splicing in the Balbiani ring 3 gene | Q39645223 |
| | Induction of exon skipping of the dystrophin transcript in lymphoblastoid cells by transfecting an antisense oligodeoxynucleotide complementary to an exon recognition sequence | Q41168085 |
| | Target selection for antisense oligonucleotide induced exon skipping in the dystrophin gene. | Q44471855 |
| | Targeted exon skipping in transgenic hDMD mice: A model for direct preclinical screening of human-specific antisense oligonucleotides | Q45007187 |
| P433 | issue | 8 | |
| P304 | page(s) | 1418-1426 | |
| P577 | publication date | 2009-03-17 | |
| P1433 | published in | Molecular Therapy | Q15762400 |
| P1476 | title | Rational design of antisense oligomers to induce dystrophin exon skipping | |
| P478 | volume | 17 | |