| review article | Q7318358 |
| scholarly article | Q13442814 |
| P356 | DOI | 10.1016/S1350-9462(03)00052-1 |
| P698 | PubMed publication ID | 14575721 |
| P50 | author | Enrico M. Surace | Q47504013 |
| Alberto Auricchio | Q56950196 | ||
| P2093 | author name string | Alberto Auricchio | |
| Enrico M Surace | |||
| P2860 | cites work | Mutational analysis of the adeno-associated virus type 2 (AAV2) capsid gene and construction of AAV2 vectors with altered tropism | Q24515072 |
| Membrane-associated heparan sulfate proteoglycan is a receptor for adeno-associated virus type 2 virions | Q24531466 | ||
| The atomic structure of adeno-associated virus (AAV-2), a vector for human gene therapy. | Q24533492 | ||
| Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy | Q24535690 | ||
| On the genetics of retinitis pigmentosa and on mutation-independent approaches to therapeutic intervention | Q24536217 | ||
| Persistent expression of human clotting factor IX from mouse liver after intravenous injection of adeno-associated virus vectors | Q24683259 | ||
| Angiogenesis in cancer and other diseases | Q27861015 | ||
| Transgenic mice with a rhodopsin mutation (Pro23His): a mouse model of autosomal dominant retinitis pigmentosa | Q28115055 | ||
| Retinal degeneration mutants in the mouse | Q28202375 | ||
| The chemical repertoire of natural ribozymes | Q30309627 | ||
| Potential long-term inhibition of ocular neovascularisation by recombinant adeno-associated virus-mediated secretion gene therapy | Q31065469 | ||
| Adeno-associated virus type-2 expression of pigmented epithelium-derived factor or Kringles 1-3 of angiostatin reduce retinal neovascularization | Q31081886 | ||
| AAV-mediated delivery of ciliary neurotrophic factor prolongs photoreceptor survival in the rhodopsin knockout mouse | Q32125104 | ||
| High-fidelity correction of mutations at multiple chromosomal positions by adeno-associated virus vectors. | Q33649500 | ||
| Birth and death in the retina: more related than we thought? | Q33703219 | ||
| Midbrain injection of recombinant adeno-associated virus encoding rat glial cell line-derived neurotrophic factor protects nigral neurons in a progressive 6-hydroxydopamine-induced degeneration model of Parkinson's disease in rats | Q33745707 | ||
| Correction of the enzymatic and functional deficits in a model of Pompe disease using adeno-associated virus vectors | Q45732679 | ||
| Neurological correction of lysosomal storage in a mucopolysaccharidosis IIIB mouse model by adeno-associated virus-mediated gene delivery | Q45734139 | ||
| Cochlear function and transgene expression in the guinea pig cochlea, using adenovirus- and adeno-associated virus-directed gene transfer. | Q45737477 | ||
| Introduction of single base substitutions at homologous chromosomal sequences by adeno-associated virus vectors | Q45737647 | ||
| Long-term real-time monitoring of adeno-associated virus-mediated gene expression in the rat retina | Q45739540 | ||
| Safety of adeno-associated virus as cochlear gene transfer vector: analysis of distant spread beyond injected cochleae | Q45740311 | ||
| Adeno-associated virus expresses transgenes in hair follicles and epidermis | Q45740674 | ||
| Additional transduction events after subretinal readministration of recombinant adeno-associated virus | Q45744116 | ||
| Genetic capsid modifications allow efficient re-targeting of adeno-associated virus type 2. | Q45745995 | ||
| Reporter expression persists 1 year after adeno-associated virus-mediated gene transfer to the optic nerve | Q45748355 | ||
| Evaluation of adeno-associated virus-mediated gene transfer into the rat retina by clinical fluorescence photography | Q45750484 | ||
| Peroral gene therapy of lactose intolerance using an adeno-associated virus vector | Q45753463 | ||
| Adeno-associated virus gene transfer to mouse retina | Q45758027 | ||
| Persistent expression of canine factor IX in hemophilia B canines | Q45862802 | ||
| Sustained production of beta-glucuronidase from localized sites after AAV vector gene transfer results in widespread distribution of enzyme and reversal of lysosomal storage lesions in a large volume of brain in mucopolysaccharidosis VII mice. | Q45864505 | ||
| Increasing the size of rAAV-mediated expression cassettes in vivo by intermolecular joining of two complementary vectors | Q45867424 | ||
| Several log increase in therapeutic transgene delivery by distinct adeno-associated viral serotype vectors | Q45873434 | ||
| Gene transfer into the mouse retina mediated by an adeno-associated viral vector | Q45877692 | ||
| Humoral response after administration of E1-deleted adenoviruses: immune privilege of the subretinal space | Q45879306 | ||
| Expanding AAV packaging capacity with trans-splicing or overlapping vectors: a quantitative comparison | Q45880308 | ||
| Chronic suppression of heart-failure progression by a pseudophosphorylated mutant of phospholamban via in vivo cardiac rAAV gene delivery | Q45888008 | ||
| Ribozyme rescue of photoreceptor cells in a transgenic rat model of autosomal dominant retinitis pigmentosa. | Q45888779 | ||
| Cochlear gene delivery through an intact round window membrane in mouse | Q46630707 | ||
| BDNF regulates the maturation of inhibition and the critical period of plasticity in mouse visual cortex | Q48104754 | ||
| Persistent transgene product in retina, optic nerve and brain after intraocular injection of rAAV. | Q48169737 | ||
| Retinal rod photoreceptor-specific gene mutation perturbs cone pathway development. | Q52175364 | ||
| Modification of glial-neuronal cell interactions prevents photoreceptor apoptosis during light-induced retinal degeneration. | Q53759609 | ||
| Intraocular gene transfer of ciliary neurotrophic factor prevents death and increases responsiveness of rod photoreceptors in the retinal degeneration slow mouse | Q60215437 | ||
| Characterization of the DNA of a defective human parvovirus isolated from a genital site | Q64380674 | ||
| Development and degeneration of retina in rds mutant mice: photoreceptor abnormalities in the heterozygotes | Q69787034 | ||
| Subunit composition of the peripherin/rds-rom-1 disk rim complex from rod photoreceptors: hydrodynamic evidence for a tetrameric quaternary structure | Q71087313 | ||
| ERG and EOG abnormalities in carriers of X-linked retinitis pigmentosa | Q71931923 | ||
| An oral vaccine against NMDAR1 with efficacy in experimental stroke and epilepsy | Q73479417 | ||
| Validation of AAV-mediated gene targeting | Q74381897 | ||
| Non-cell-autonomous photoreceptor degeneration in rds mutant mice mosaic for expression of a rescue transgene | Q74562756 | ||
| Inhibition of retinal neovascularization by intraocular viral-mediated delivery of anti-angiogenic agents | Q78365092 | ||
| Adeno-associated virus type 5 (AAV5) but not AAV2 binds to the apical surfaces of airway epithelia and facilitates gene transfer | Q33802811 | ||
| An AAV-derived Apaf-1 dominant negative inhibitor prevents MPTP toxicity as antiapoptotic gene therapy for Parkinson's disease | Q33943954 | ||
| Retinal and choroidal neovascularization | Q33980639 | ||
| Gene therapy for ocular disease | Q33996515 | ||
| Ribozyme uses in retinal gene therapy. | Q34058780 | ||
| Gene therapy and retinitis pigmentosa: advances and future challenges | Q34084443 | ||
| Retinitis pigmentosa and allied diseases: numerous diseases, genes, and inheritance patterns. | Q34128761 | ||
| Clinical protocol. Gene therapy of Canavan disease: AAV-2 vector for neurosurgical delivery of aspartoacylase gene (ASPA) to the human brain | Q34142832 | ||
| Long-term systemic therapy of Fabry disease in a knockout mouse by adeno-associated virus-mediated muscle-directed gene transfer | Q34161415 | ||
| AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B. | Q34168942 | ||
| Pathways to photoreceptor cell death in inherited retinal degenerations | Q34312941 | ||
| Virus-mediated transduction of murine retina with adeno-associated virus: effects of viral capsid and genome size. | Q34342913 | ||
| Apoptosis: final common pathway of photoreceptor death in rd, rds, and rhodopsin mutant mice | Q34357143 | ||
| Gene therapy for hemophilia B: AAV-mediated transfer of the gene for coagulation factor IX to human muscle. | Q34367815 | ||
| AlphaVbeta5 integrin: a co-receptor for adeno-associated virus type 2 infection | Q34486863 | ||
| Molecular genetics of Leber congenital amaurosis | Q34641603 | ||
| Vascular endothelial growth factor/vascular permeability factor expression in a mouse model of retinal neovascularization | Q34749337 | ||
| Noninvasive gene transfer to the lung for systemic delivery of therapeutic proteins. | Q34777289 | ||
| Canine inherited retinal degenerations: update on molecular genetic research and its clinical application | Q34980394 | ||
| Gene delivery to the eye using adeno-associated viral vectors | Q34987213 | ||
| Site-specific integration mediated by a hybrid adenovirus/adeno-associated virus vector. | Q35057135 | ||
| Recombinant adeno-associated virus type 2, 4, and 5 vectors: transduction of variant cell types and regions in the mammalian central nervous system. | Q35111738 | ||
| Ribozyme rescue of photoreceptor cells in P23H transgenic rats: long-term survival and late-stage therapy. | Q35306158 | ||
| Trans-splicing vectors expand the utility of adeno-associated virus for gene therapy | Q35799349 | ||
| Defective subunit assembly underlies a digenic form of retinitis pigmentosa linked to mutations in peripherin/rds and rom-1. | Q35926100 | ||
| Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus | Q36159178 | ||
| Normal retina releases a diffusible factor stimulating cone survival in the retinal degeneration mouse | Q36175279 | ||
| Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus | Q36242842 | ||
| Stable transgene expression in rod photoreceptors after recombinant adeno-associated virus-mediated gene transfer to monkey retina | Q36439639 | ||
| Sustained correction of bleeding disorder in hemophilia B mice by gene therapy | Q36454880 | ||
| Deficiency of rds/peripherin causes photoreceptor death in mouse models of digenic and dominant retinitis pigmentosa | Q36520157 | ||
| Stable and efficient gene transfer into the retina using an HIV-based lentiviral vector | Q36586077 | ||
| Adeno-associated viral-mediated catalase expression suppresses optic neuritis in experimental allergic encephalomyelitis | Q36802175 | ||
| Neonatal gene transfer leads to widespread correction of pathology in a murine model of lysosomal storage disease. | Q37181003 | ||
| Site-specific integration by adeno-associated virus | Q37246710 | ||
| bcl-2 overexpression reduces apoptotic photoreceptor cell death in three different retinal degenerations | Q37484075 | ||
| Site-specific integration of a transgene mediated by a hybrid adenovirus/adeno-associated virus vector using the Cre/loxP-expression-switching system | Q38310905 | ||
| Hybrid vectors based on adeno-associated virus serotypes 2 and 5 for muscle-directed gene transfer | Q39603323 | ||
| Enhancement of muscle gene delivery with pseudotyped adeno-associated virus type 5 correlates with myoblast differentiation. | Q39606539 | ||
| Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity | Q39686097 | ||
| Filovirus-pseudotyped lentiviral vector can efficiently and stably transduce airway epithelia in vivo | Q40606944 | ||
| Adeno-associated virus: a vector system for efficient introduction and integration of DNA into a variety of mammalian cell types | Q40660263 | ||
| Gene therapy strategy for long-term myocardial protection using adeno-associated virus-mediated delivery of heme oxygenase gene | Q40662320 | ||
| Glial cell line derived neurotrophic factor delays photoreceptor degeneration in a transgenic rat model of retinitis pigmentosa | Q40764969 | ||
| Recombinant AAV-mediated delivery of a tet-inducible reporter gene to the rat retina | Q40805811 | ||
| Two animal models of retinal degeneration are rescued by recombinant adeno-associated virus-mediated production of FGF-5 and FGF-18. | Q40810201 | ||
| Triple transduction with adeno-associated virus vectors expressing tyrosine hydroxylase, aromatic-L-amino-acid decarboxylase, and GTP cyclohydrolase I for gene therapy of Parkinson's disease | Q40861090 | ||
| Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy. | Q40869164 | ||
| Green fluorescent protein as a reporter for gene transfer studies in the cochlea | Q40871576 | ||
| Targeted adeno-associated virus vector transduction of nonpermissive cells mediated by a bispecific F(ab'gamma)2 antibody | Q40969562 | ||
| Adeno-associated virus expression systems for gene transfer | Q40994121 | ||
| Encapsidated adenovirus mini-chromosome-mediated delivery of genes to the retina: application to the rescue of photoreceptor degeneration | Q40995318 | ||
| Structural and functional heterogeneity of integrated recombinant AAV genomes | Q41118391 | ||
| Lack of site-specific integration of the recombinant adeno-associated virus 2 genomes in human cells | Q41128137 | ||
| Human gene targeting by viral vectors | Q41480639 | ||
| Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector. | Q41722852 | ||
| Sustained expression of therapeutic level of factor IX in hemophilia B dogs by AAV-mediated gene therapy in liver | Q41753510 | ||
| Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain | Q42280576 | ||
| Adenoviral and adeno-associated viral vector mediated gene transfer in the guinea pig cochlea | Q42524407 | ||
| Pharmacologically regulated gene expression in the retina following transduction with viral vectors | Q43583263 | ||
| Adenovirus-mediated delivery of rhodopsin-promoted bcl-2 results in a delay in photoreceptor cell death in the rd/rd mouse | Q43656038 | ||
| Functional effect of adeno-associated virus mediated gene transfer of aromatic L-amino acid decarboxylase into the striatum of 6-OHDA-lesioned rats. | Q43707952 | ||
| Long-term protection of retinal structure but not function using RAAV.CNTF in animal models of retinitis pigmentosa | Q43715205 | ||
| Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors | Q43716886 | ||
| Gene replacement therapy in the retinal degeneration slow (rds) mouse: the effect on retinal degeneration following partial transduction of the retina | Q43786764 | ||
| Exchange of surface proteins impacts on viral vector cellular specificity and transduction characteristics: the retina as a model | Q43829645 | ||
| A deviant immune response to viral proteins and transgene product is generated on subretinal administration of adenovirus and adeno-associated virus | Q43877928 | ||
| Behavioral recovery in a primate model of Parkinson's disease by triple transduction of striatal cells with adeno-associated viral vectors expressing dopamine-synthesizing enzymes | Q43892747 | ||
| Baculoviral IAP repeat-containing-4 protects optic nerve axons in a rat glaucoma model | Q44003999 | ||
| Effects of adeno-associated virus-vectored ciliary neurotrophic factor on retinal structure and function in mice with a P216L rds/peripherin mutation | Q44070483 | ||
| Pharmacological regulation of protein expression from adeno-associated viral vectors in the eye. | Q44088681 | ||
| Evidence for two apoptotic pathways in light-induced retinal degeneration | Q44130152 | ||
| Long-term in vivo cochlear transgene expression mediated by recombinant adeno-associated virus | Q44136141 | ||
| Intravitreal injection of adeno-associated viral vectors results in the transduction of different types of retinal neurons in neonatal and adult rats: a comparison with lentiviral vectors. | Q44163861 | ||
| Rescue of a mitochondrial deficiency causing Leber Hereditary Optic Neuropathy | Q44195721 | ||
| Phenotypic rescue after adeno-associated virus-mediated delivery of 4-sulfatase to the retinal pigment epithelium of feline mucopolysaccharidosis VI. | Q44221630 | ||
| Efficient trans-splicing in the retina expands the utility of adeno-associated virus as a vector for gene therapy. | Q44305893 | ||
| Inhibition of retinal neovascularisation by gene transfer of soluble VEGF receptor sFlt-1. | Q44763476 | ||
| Direct intramuscular injection with recombinant AAV vectors results in sustained expression in a dog model of hemophilia | Q45060641 | ||
| Kinetics of transgene expression in mouse retina following sub-retinal injection of recombinant adeno-associated virus | Q45712572 | ||
| The adeno-associated virus crystal: impact inversely proportional to size | Q45730485 | ||
| P433 | issue | 6 | |
| P304 | page(s) | 705-719 | |
| P577 | publication date | 2003-11-01 | |
| P1433 | published in | Progress in Retinal and Eye Research | Q15760062 |
| P1476 | title | Adeno-associated viral vectors for retinal gene transfer | |
| P478 | volume | 22 |
| Q38585967 | AAV mediated GDNF secretion from retinal glia slows down retinal degeneration in a rat model of retinitis pigmentosa |
| Q45858441 | AAV-mediated expression of CNTF promotes long-term survival and regeneration of adult rat retinal ganglion cells |
| Q36708300 | AAV-mediated gene transfer for retinal diseases |
| Q37301637 | AAV-mediated local delivery of interferon-beta for the treatment of retinoblastoma in preclinical models |
| Q36165834 | Adeno-associated virus vectors: potential applications for cancer gene therapy |
| Q46603658 | Amelioration of both functional and morphological abnormalities in the retina of a mouse model of ocular albinism following AAV-mediated gene transfer |
| Q37987054 | Cell-replacement therapy and neural repair in the retina |
| Q42840509 | Changes in adeno-associated virus-mediated gene delivery in retinal degeneration |
| Q39507783 | Comparison of the transduction efficiency of tyrosine-mutant adeno-associated virus serotype vectors in kidney |
| Q43065525 | Evaluation of the adeno-associated virus mediated long-term expression of channelrhodopsin-2 in the mouse retina |
| Q43581890 | Fluorescein angiographic findings in eyes of patients with a subretinal electronic implant |
| Q38153722 | Gene therapy in corneal transplantation |
| Q33713361 | High-efficiency transduction of the mouse retina by tyrosine-mutant AAV serotype vectors |
| Q36580252 | In vitro analysis of promoter activity in Müller cells |
| Q27332143 | MicroRNA-restricted transgene expression in the retina |
| Q39733465 | Nanomaterials in controlled drug release |
| Q35892036 | Parallel processing in the mammalian retina |
| Q45417238 | Safety of recombinant adeno-associated virus type 2-RPE65 vector delivered by ocular subretinal injection |
| Q36904857 | Strategies for blocking angiogenesis in diabetic retinopathy: from basic science to clinical practice |
| Q36965152 | Versatility of AAV vectors for retinal gene transfer |
| Q31120899 | rAAV-mediated subcellular targeting of optogenetic tools in retinal ganglion cells in vivo |
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