| scholarly article | Q13442814 |
| review article | Q7318358 |
| P2093 | author name string | Rajendra Kumar-Singh | |
| P2860 | cites work | Gene therapy -- promises, problems and prospects | Q45883584 |
| phiC31 integrase confers genomic integration and long-term transgene expression in rat retina | Q45883736 | ||
| Gene replacement therapy rescues photoreceptor degeneration in a murine model of Leber congenital amaurosis lacking RPGRIP. | Q45886246 | ||
| Stable and efficient intraocular gene transfer using pseudotyped EIAV lentiviral vectors | Q45888728 | ||
| Tissue-specific and developmental regulation of rod opsin chimeric genes in transgenic mice | Q45967554 | ||
| AAV vectors and tumorigenicity | Q46266970 | ||
| Immune responses against tetracycline-dependent transactivators affect long-term expression of mouse erythropoietin delivered by a helper-dependent adenoviral vector | Q46385266 | ||
| Mouse models of ocular diseases | Q46839093 | ||
| Adenoviral vector-delivered pigment epithelium-derived factor for neovascular age-related macular degeneration: results of a phase I clinical trial | Q46924646 | ||
| Improved retinal transduction in vivo and photoreceptor-specific transgene expression using adenovirus vectors with modified penton base | Q50683565 | ||
| Cell-mediated immune response and stability of intraocular transgene expression after adenovirus-mediated delivery | Q56908168 | ||
| Organ-specific expression of the lacZ gene controlled by the opsin promoter after intravenous gene administration in adult mice | Q57677348 | ||
| Right timing for retina repair | Q59068908 | ||
| Update on adenovirus and its vectors | Q64380348 | ||
| A differential efficiency of adenovirus-mediated in vivo gene transfer into skeletal muscle cells of different maturity | Q64383574 | ||
| Cell death in the development of the human retina: phagocytosis of pyknotic and apoptotic bodies by retinal cells | Q70157413 | ||
| Apoptosis during development of the human retina: relationship to foveal development and retinal synaptogenesis | Q73089906 | ||
| Murine leukemia induced by retroviral gene marking | Q77975543 | ||
| Clinical trials. Gene transfer an unlikely contributor to patient's death | Q80156793 | ||
| Selective cell uptake of modified Tat peptide-fluorophore conjugates in rat retina in ex vivo and in vivo models | Q83839678 | ||
| DAI (DLM-1/ZBP1) is a cytosolic DNA sensor and an activator of innate immune response | Q24317784 | ||
| Site-specific integration by adeno-associated virus | Q24558738 | ||
| Safety and efficacy of gene transfer for Leber's congenital amaurosis | Q24634724 | ||
| A retinitis pigmentosa GTPase regulator (RPGR)-deficient mouse model for X-linked retinitis pigmentosa (RP3) | Q24676561 | ||
| A hybrid photoreceptor expressing both rod and cone genes in a mouse model of enhanced S-cone syndrome. | Q24813359 | ||
| Pathogen recognition and innate immunity | Q27861084 | ||
| Transgenic mice with a rhodopsin mutation (Pro23His): a mouse model of autosomal dominant retinitis pigmentosa | Q28115055 | ||
| Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease | Q28143064 | ||
| Effect of gene therapy on visual function in Leber's congenital amaurosis | Q28277981 | ||
| Photoreceptor cell rescue in retinal degeneration (rd) mice by in vivo gene therapy | Q28279907 | ||
| A versatile vector for gene and oligonucleotide transfer into cells in culture and in vivo: polyethylenimine | Q29616154 | ||
| Retinitis pigmentosa | Q29616538 | ||
| Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response | Q29619095 | ||
| Long-term transgene expression in the RPE after gene transfer with a high-capacity adenoviral vector | Q31064383 | ||
| The relationship between opsin overexpression and photoreceptor degeneration | Q32061867 | ||
| D-TAT transporter as an ocular peptide delivery system | Q33231239 | ||
| Efficient non-viral ocular gene transfer with compacted DNA nanoparticles | Q33267297 | ||
| Cell fate determination in the vertebrate retina | Q33564487 | ||
| Large-scale molecular characterization of adeno-associated virus vector integration in mouse liver | Q33737640 | ||
| Lifetime correction of genetic deficiency in mice with a single injection of helper-dependent adenoviral vector | Q33949311 | ||
| Cell-penetrating peptide for enhanced delivery of nucleic acids and drugs to ocular tissues including retina and cornea | Q34093606 | ||
| Absence of functional and structural abnormalities associated with expression of EGFP in the retina | Q34120983 | ||
| Characterization of adeno-associated virus genomes isolated from human tissues | Q34142848 | ||
| Immune response following intraocular delivery of recombinant viral vectors | Q34198445 | ||
| Rhodopsin signaling and organization in heterozygote rhodopsin knockout mice | Q34313774 | ||
| Recombinant AAV-mediated gene transfer to the retina: gene therapy perspectives | Q34354096 | ||
| Effective gene therapy with nonintegrating lentiviral vectors | Q34496367 | ||
| Response of retinoblastoma with vitreous tumor seeding to adenovirus-mediated delivery of thymidine kinase followed by ganciclovir | Q34562176 | ||
| HSV-1 VP22 augments adenoviral gene transfer to CNS neurons in the retina and striatum in vivo | Q44420163 | ||
| Nanoparticles of compacted DNA transfect postmitotic cells | Q44478822 | ||
| Organ-specific gene expression in the rhesus monkey eye following intravenous non-viral gene transfer | Q44613306 | ||
| Adenoviral-mediated gene transfer to retinal explants during development and degeneration | Q44706879 | ||
| Efficient gene transfer into retinal cells using adenoviral vectors: dependence on receptor expression | Q44909595 | ||
| Rescue of photoreceptor function by AAV-mediated gene transfer in a mouse model of inherited retinal degeneration | Q44933268 | ||
| Observed incidence of tumorigenesis in long-term rodent studies of rAAV vectors. | Q44974380 | ||
| Long-term preservation of retinal function in the RCS rat model of retinitis pigmentosa following lentivirus-mediated gene therapy | Q45230950 | ||
| Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors | Q45299117 | ||
| Does recombinant adeno-associated virus-vectored proximal region of mouse rhodopsin promoter support only rod-type specific expression in vivo? | Q45417651 | ||
| Postsurgical assessment and long-term safety of recombinant adeno-associated virus-mediated gene transfer into the retinas of dogs and primates | Q45483961 | ||
| Recombinant adeno-associated virus for muscle directed gene therapy | Q45764433 | ||
| Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector | Q45855552 | ||
| Long-term doxycycline-regulated transgene expression in the retina of nonhuman primates following subretinal injection of recombinant AAV vectors | Q45855564 | ||
| Gene therapy. Seeking the cause of induced leukemias in X-SCID trial | Q45858033 | ||
| Immune responses limit adenovirally mediated gene expression in the adult mouse eye. | Q45858160 | ||
| Efficiency of lentiviral transduction during development in normal and rd mice | Q45861263 | ||
| Gene transfer to rabbit retina with electron avalanche transfection | Q45862041 | ||
| Restoration of vision in RPE65-deficient Briard dogs using an AAV serotype 4 vector that specifically targets the retinal pigmented epithelium | Q45863029 | ||
| Gene therapy death prompts review of adenovirus vector | Q45864618 | ||
| AAV vector integration sites in mouse hepatocellular carcinoma. | Q45869780 | ||
| Helper-dependent adenovirus for the gene therapy of proliferative retinopathies: stable gene transfer, regulated gene expression and therapeutic efficacy | Q45870051 | ||
| AAV-mediated expression targeting of rod and cone photoreceptors with a human rhodopsin kinase promoter | Q45870501 | ||
| Gene transfer into the mouse retina mediated by an adeno-associated viral vector | Q45877692 | ||
| Gene therapy. Viral vectors still pack surprises | Q45881684 | ||
| Lineage analysis in the vertebrate nervous system by retrovirus-mediated gene transfer | Q34585324 | ||
| A helper-dependent adenovirus vector system: removal of helper virus by Cre-mediated excision of the viral packaging signal | Q35915922 | ||
| Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein | Q35943644 | ||
| Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors | Q36099346 | ||
| Regulatable gene expression systems for gene therapy applications: progress and future challenges | Q36157542 | ||
| An adenoviral vector deleted for all viral coding sequences results in enhanced safety and extended expression of a leptin transgene | Q36163092 | ||
| Adeno-associated viral vectors for retinal gene transfer and treatment of retinal diseases | Q36173008 | ||
| Translocation of RNA-coated gold particles through the nuclear pores of oocytes | Q36218652 | ||
| Stable transgene expression in rod photoreceptors after recombinant adeno-associated virus-mediated gene transfer to monkey retina | Q36439639 | ||
| One-year expression from high-capacity adenoviral vectors in the brains of animals with pre-existing anti-adenoviral immunity: clinical implications. | Q36498762 | ||
| Signal-mediated nuclear transport in proliferating and growth-arrested BALB/c 3T3 cells | Q36532926 | ||
| Gene therapy progress and prospects: the eye. | Q36534765 | ||
| Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice. | Q36545533 | ||
| Administration of helper-dependent adenoviral vectors and sequential delivery of different vector serotype for long-term liver-directed gene transfer in baboons | Q36557727 | ||
| Stable and efficient gene transfer into the retina using an HIV-based lentiviral vector | Q36586077 | ||
| AAV-mediated gene transfer for retinal diseases | Q36708300 | ||
| Evidence for covalent attachment of the adeno-associated virus (AAV) rep protein to the ends of the AAV genome | Q36796289 | ||
| Gene therapy clinical trials worldwide to 2007--an update. | Q36920192 | ||
| Versatility of AAV vectors for retinal gene transfer | Q36965152 | ||
| Efficient in vivo gene expression by trans-splicing adeno-associated viral vectors | Q36968876 | ||
| Immune responses to gene product of inducible promoters | Q36990105 | ||
| Development of photoreceptor-specific promoters and their utility to investigate EIAV lentiviral vector mediated gene transfer to photoreceptors | Q38297007 | ||
| A helper-dependent capsid-modified adenovirus vector expressing adeno-associated virus rep78 mediates site-specific integration of a 27-kilobase transgene cassette | Q39320579 | ||
| Rescue from photoreceptor degeneration in the rd mouse by human immunodeficiency virus vector-mediated gene transfer | Q39551137 | ||
| Integration of adenovirus type 2 DNA at a limited number of cellular sites in productively infected cells | Q39813512 | ||
| Nanoparticles for gene delivery to retinal pigment epithelial cells. | Q40442338 | ||
| Rhodopsin-iCre transgenic mouse line for Cre-mediated rod-specific gene targeting. | Q40449714 | ||
| Improved system for helper-dependent adenoviral vector production | Q40619668 | ||
| Intercellular trafficking of adenovirus-delivered HSV VP22 from the retinal pigment epithelium to the photoreceptors--implications for gene therapy | Q40681468 | ||
| Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy. | Q40869164 | ||
| Encapsidated adenovirus mini-chromosome-mediated delivery of genes to the retina: application to the rescue of photoreceptor degeneration | Q40995318 | ||
| Lack of site-specific integration of the recombinant adeno-associated virus 2 genomes in human cells | Q41128137 | ||
| Encapsidated adenovirus minichromosomes allow delivery and expression of a 14 kb dystrophin cDNA to muscle cells | Q41187750 | ||
| Evidence of protein transduction but not intercellular transport by proteins fused to HIV tat in retinal cell culture and in vivo | Q42168186 | ||
| Compacted DNA nanoparticles administered to the nasal mucosa of cystic fibrosis subjects are safe and demonstrate partial to complete cystic fibrosis transmembrane regulator reconstitution | Q42473767 | ||
| A burst of differentiation in the outer posterior retina of the eleven-week human fetus: an ultrastructural study. | Q42482893 | ||
| Gene therapy restores vision in a canine model of childhood blindness | Q43590733 | ||
| Gene replacement therapy in the retinal degeneration slow (rds) mouse: the effect on retinal degeneration following partial transduction of the retina | Q43786764 | ||
| Retinal cell type expression specificity of HIV-1-derived gene transfer vectors upon subretinal injection in the adult rat: influence of pseudotyping and promoter. | Q43833846 | ||
| In vivo gene transfer to the mouse eye using an HIV-based lentiviral vector; efficient long-term transduction of corneal endothelium and retinal pigment epithelium | Q43917989 | ||
| Widespread expression of an exogenous gene in the eye after intravenous administration. | Q44119141 | ||
| In vivo transduction of photoreceptors or ciliary body by intravitreal injection of pseudotyped adenoviral vectors | Q44306365 | ||
| Functional and structural recovery of the retina after gene therapy in the RPE65 null mutation dog. | Q44376450 | ||
| P433 | issue | 16 | |
| P921 | main subject | gene therapy | Q213901 |
| P304 | page(s) | 1671-1680 | |
| P577 | publication date | 2008-06-18 | |
| P1433 | published in | Vision Research | Q1307852 |
| P1476 | title | Barriers for retinal gene therapy: separating fact from fiction | |
| P478 | volume | 48 |
| Q34093683 | A poly(ethylene) glycolylated peptide for ocular delivery compacts DNA into nanoparticles for gene delivery to post-mitotic tissues in vivo |
| Q38862505 | Application of lipid nanoparticles to ocular drug delivery |
| Q35663857 | Gene Therapy of ABCA4-Associated Diseases |
| Q38122108 | Gene replacement therapy for retinal CNG channelopathies |
| Q37942753 | Gene therapy for retinal ganglion cell neuroprotection in glaucoma |
| Q27009261 | Gene therapy of inherited retinal degenerations: prospects and challenges |
| Q36147481 | Gene therapy of inherited retinopathies: a long and successful road from viral vectors to patients |
| Q37945218 | Gene therapy with helper-dependent adenoviral vectors: current advances and future perspectives |
| Q37582126 | Helper-Dependent Adenoviral Vectors. |
| Q64228294 | Immune Response and Intraocular Inflammation in Patients With Leber Hereditary Optic Neuropathy Treated With Intravitreal Injection of Recombinant Adeno-Associated Virus 2 Carrying the ND4 Gene: A Secondary Analysis of a Phase 1/2 Clinical Trial |
| Q38515294 | Lentiviral vectors as tools to understand central nervous system biology in mammalian model organisms. |
| Q35546692 | Long-term RNA interference gene therapy in a dominant retinitis pigmentosa mouse model |
| Q48735724 | Measuring the intravitreal mobility of nanomedicines with single-particle tracking microscopy |
| Q37899932 | Non-viral retinal gene therapy: a review |
| Q45882673 | Prospects for gene therapy of inherited retinal disease |
| Q42208596 | Retinal transduction profiles by high-capacity viral vectors |
| Q35073956 | Subretinal gene delivery using helper-dependent adenoviral vectors. |
| Q42548280 | Sustained gene expression in the retina by improved episomal vectors |
| Q41538270 | USH2A Gene Editing Using the CRISPR System |
| Q34561531 | Vector platforms for gene therapy of inherited retinopathies. |
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