Gene therapy to rescue retinal degeneration caused by mutations in rhodopsin.

scientific article

Gene therapy to rescue retinal degeneration caused by mutations in rhodopsin. is …
instance of (P31):
scholarly articleQ13442814

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P356DOI10.1007/978-1-4939-2330-4_25
P8608Fatcat IDrelease_nppcewwo5zf4vnty7tfq42whbq
P932PMC publication ID4696870
P698PubMed publication ID25697537
P5875ResearchGate publication ID272518138

P50authorAlfred S. LewinQ42708657
P2093author name stringRenee C Ryals
Brian P Rossmiller
P2860cites workGene therapy in animal models of autosomal dominant retinitis pigmentosaQ38053151
The cell stress machinery and retinal degenerationQ38107689
Production and purification of serotype 1, 2, and 5 recombinant adeno-associated viral vectorsQ40692830
Long-term rescue of retinal structure and function by rhodopsin RNA replacement with a single adeno-associated viral vector in P23H RHO transgenic mice.Q42003725
Mutation-independent rescue of a novel mouse model of Retinitis PigmentosaQ42032781
Production and purification of recombinant adeno-associated vectorsQ45874484
Functional abnormalities in transgenic mice expressing a mutant rhodopsin geneQ72410745
Rapid quantification of adult and developing mouse spatial vision using a virtual optomotor systemQ81041523
Case 15-2009: a man with coma after cardiac arrestQ95802924
Mechanisms of cell death in rhodopsin retinitis pigmentosa: implications for therapyQ21710681
Vision 1 year after gene therapy for Leber's congenital amaurosisQ24607981
Treatment of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trialQ24608049
Human RPE65 gene therapy for Leber congenital amaurosis: persistence of early visual improvements and safety at 1 yearQ24634801
A hybrid vector system expands adeno-associated viral vector packaging capacity in a transgene-independent mannerQ28256353
Speed, spatial, and temporal tuning of rod and cone vision in mouseQ28587151
Zinc-finger-based transcriptional repression of rhodopsin in a model of dominant retinitis pigmentosaQ30499972
Suppression and replacement gene therapy for autosomal dominant disease in a murine model of dominant retinitis pigmentosaQ34158497
Adeno-associated virus vectorology, manufacturing, and clinical applicationsQ34172314
Efficient transgene reconstitution with hybrid dual AAV vectors carrying the minimized bridging sequencesQ34511733
Identification of disease-causing mutations in autosomal dominant retinitis pigmentosa (adRP) using next-generation DNA sequencingQ34646786
Targeting photoreceptors via intravitreal delivery using novel, capsid-mutated AAV vectorsQ34700925
Self-complementary AAV vectors; advances and applicationsQ34804660
Antioxidants reduce cone cell death in a model of retinitis pigmentosaQ34983972
Long-term characterization of retinal degeneration in rd1 and rd10 mice using spectral domain optical coherence tomographyQ36089356
Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virusQ36242842
Viral serotype and the transgene sequence influence overlapping adeno-associated viral (AAV) vector-mediated gene transfer in skeletal muscleQ36968848
Adeno-associated viral vectors and the retinaQ37055045
Clinical gene therapy using recombinant adeno-associated virus vectorsQ37140649
The gene therapy revolution in ophthalmologyQ37258541
Effective delivery of large genes to the retina by dual AAV vectorsQ37591108
P407language of work or nameEnglishQ1860
P921main subjectgene therapyQ213901
retinal degenerationQ3043268
P304page(s)391-410
P577publication date2015-01-01
P1433published inMethods in Molecular BiologyQ15752859
P1476titleGene therapy to rescue retinal degeneration caused by mutations in rhodopsin
P478volume1271

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cites work (P2860)
Q93016526Has retinal gene therapy come of age? From bench to bedside and back to bench
Q36097231Human β-NGF gene transferred to cat corneal endothelial cells

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