scholarly article | Q13442814 |
P356 | DOI | 10.1007/978-1-4939-2330-4_25 |
P8608 | Fatcat ID | release_nppcewwo5zf4vnty7tfq42whbq |
P932 | PMC publication ID | 4696870 |
P698 | PubMed publication ID | 25697537 |
P5875 | ResearchGate publication ID | 272518138 |
P50 | author | Alfred S. Lewin | Q42708657 |
P2093 | author name string | Renee C Ryals | |
Brian P Rossmiller | |||
P2860 | cites work | Gene therapy in animal models of autosomal dominant retinitis pigmentosa | Q38053151 |
The cell stress machinery and retinal degeneration | Q38107689 | ||
Production and purification of serotype 1, 2, and 5 recombinant adeno-associated viral vectors | Q40692830 | ||
Long-term rescue of retinal structure and function by rhodopsin RNA replacement with a single adeno-associated viral vector in P23H RHO transgenic mice. | Q42003725 | ||
Mutation-independent rescue of a novel mouse model of Retinitis Pigmentosa | Q42032781 | ||
Production and purification of recombinant adeno-associated vectors | Q45874484 | ||
Functional abnormalities in transgenic mice expressing a mutant rhodopsin gene | Q72410745 | ||
Rapid quantification of adult and developing mouse spatial vision using a virtual optomotor system | Q81041523 | ||
Case 15-2009: a man with coma after cardiac arrest | Q95802924 | ||
Mechanisms of cell death in rhodopsin retinitis pigmentosa: implications for therapy | Q21710681 | ||
Vision 1 year after gene therapy for Leber's congenital amaurosis | Q24607981 | ||
Treatment of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trial | Q24608049 | ||
Human RPE65 gene therapy for Leber congenital amaurosis: persistence of early visual improvements and safety at 1 year | Q24634801 | ||
A hybrid vector system expands adeno-associated viral vector packaging capacity in a transgene-independent manner | Q28256353 | ||
Speed, spatial, and temporal tuning of rod and cone vision in mouse | Q28587151 | ||
Zinc-finger-based transcriptional repression of rhodopsin in a model of dominant retinitis pigmentosa | Q30499972 | ||
Suppression and replacement gene therapy for autosomal dominant disease in a murine model of dominant retinitis pigmentosa | Q34158497 | ||
Adeno-associated virus vectorology, manufacturing, and clinical applications | Q34172314 | ||
Efficient transgene reconstitution with hybrid dual AAV vectors carrying the minimized bridging sequences | Q34511733 | ||
Identification of disease-causing mutations in autosomal dominant retinitis pigmentosa (adRP) using next-generation DNA sequencing | Q34646786 | ||
Targeting photoreceptors via intravitreal delivery using novel, capsid-mutated AAV vectors | Q34700925 | ||
Self-complementary AAV vectors; advances and applications | Q34804660 | ||
Antioxidants reduce cone cell death in a model of retinitis pigmentosa | Q34983972 | ||
Long-term characterization of retinal degeneration in rd1 and rd10 mice using spectral domain optical coherence tomography | Q36089356 | ||
Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus | Q36242842 | ||
Viral serotype and the transgene sequence influence overlapping adeno-associated viral (AAV) vector-mediated gene transfer in skeletal muscle | Q36968848 | ||
Adeno-associated viral vectors and the retina | Q37055045 | ||
Clinical gene therapy using recombinant adeno-associated virus vectors | Q37140649 | ||
The gene therapy revolution in ophthalmology | Q37258541 | ||
Effective delivery of large genes to the retina by dual AAV vectors | Q37591108 | ||
P407 | language of work or name | English | Q1860 |
P921 | main subject | gene therapy | Q213901 |
retinal degeneration | Q3043268 | ||
P304 | page(s) | 391-410 | |
P577 | publication date | 2015-01-01 | |
P1433 | published in | Methods in Molecular Biology | Q15752859 |
P1476 | title | Gene therapy to rescue retinal degeneration caused by mutations in rhodopsin | |
P478 | volume | 1271 |
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