| scholarly article | Q13442814 |
| P50 | author | Hannah E Wand | Q87623209 |
| P2093 | author name string | Edward Smith | |
| Sharon E Hesterlee | |||
| Valeria Ricotti | |||
| Carol Mansfield | |||
| Janice P Tzeng | |||
| Carl Morris | |||
| Ryan Fischer | |||
| Katherine Beaverson | |||
| Holly Landrum Peay | |||
| Amy Strong Martin | |||
| Colin Rensch | |||
| P2860 | cites work | The burden, epidemiology, costs and treatment for Duchenne muscular dystrophy: an evidence review | Q30234649 |
| NBD delivery improves the disease phenotype of the golden retriever model of Duchenne muscular dystrophy | Q35190356 | ||
| "Watching time tick by…": Decision making for Duchenne muscular dystrophy trials | Q36691404 | ||
| Quantifying the burden of caregiving in Duchenne muscular dystrophy | Q36879404 | ||
| Mothers' psychological adaptation to Duchenne/Becker muscular dystrophy | Q37058533 | ||
| Burden, professional support, and social network in families of children and young adults with muscular dystrophies. | Q37269549 | ||
| Follistatin Gene Therapy Improves Ambulation in Becker Muscular Dystrophy | Q37589700 | ||
| Expectations and experiences of investigators and parents involved in a clinical trial for Duchenne/Becker muscular dystrophy. | Q37604269 | ||
| Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management | Q37640907 | ||
| Duchenne and Becker muscular dystrophies. | Q38230979 | ||
| Barriers and facilitators to clinical trial participation among parents of children with pediatric neuromuscular disorders | Q64046215 | ||
| Depression in parents of children with Duchenne muscular dystrophy | Q80321738 | ||
| Regarding "Eteplirsen for the treatment of Duchenne muscular dystrophy" | Q89023608 | ||
| Deflazacort approved for Duchenne muscular dystrophy | Q89443818 | ||
| How Do Members of the Duchenne and Becker Muscular Dystrophy Community Perceive a Discrete-Choice Experiment Incorporating Uncertain Treatment Benefit? An Application of Research as an Event | Q91796362 | ||
| Predictors of Health-Related Quality of Life in boys with Duchenne muscular dystrophy from six European countries | Q38760121 | ||
| Exon skipping: a first in class strategy for Duchenne muscular dystrophy | Q38784820 | ||
| Patient-centered benefit-risk assessment in duchenne muscular dystrophy | Q38959668 | ||
| Developing a Patient-Centered Benefit-Risk Survey: A Community-Engaged Process | Q38973870 | ||
| Caregiver preferences for emerging duchenne muscular dystrophy treatments: a comparison of best-worst scaling and conjoint analysis | Q39071862 | ||
| Advances in the Treatment of Duchenne Muscular Dystrophy: New and Emerging Pharmacotherapies | Q39115626 | ||
| Progress toward Gene Therapy for Duchenne Muscular Dystrophy | Q39246797 | ||
| Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy. | Q40109350 | ||
| Phase I study of dystrophin plasmid-based gene therapy in Duchenne/Becker muscular dystrophy. | Q40459778 | ||
| Muscle function recovery in golden retriever muscular dystrophy after AAV1-U7 exon skipping. | Q41136552 | ||
| Dystrophin immunity in Duchenne's muscular dystrophy. | Q41590387 | ||
| FDA Approves Eteplirsen for Duchenne Muscular Dystrophy: The Next Chapter in the Eteplirsen Saga | Q42214158 | ||
| The effect of caregiving on women in families with Duchenne/Becker muscular dystrophy | Q44551642 | ||
| Developing standardized corticosteroid treatment for Duchenne muscular dystrophy. | Q45281605 | ||
| A community-engaged approach to quantifying caregiver preferences for the benefits and risks of emerging therapies for Duchenne muscular dystrophy | Q46505109 | ||
| An Evidence-Based, Community-Engaged Approach to Develop an Interactive Deliberation Tool for Pediatric Neuromuscular Trials | Q47278796 | ||
| Prioritizing Parental Worry Associated with Duchenne Muscular Dystrophy Using Best-Worst Scaling | Q47657270 | ||
| Health-related quality of life in children and adolescents with Duchenne muscular dystrophy | Q48360412 | ||
| Hidden consequences of success in pediatrics: parental health-related quality of life--results from the Care Project | Q48421330 | ||
| Subjective caregiver burden of parents of adults with Duchenne muscular dystrophy. | Q48525393 | ||
| P275 | copyright license | Creative Commons Attribution 4.0 International | Q20007257 |
| P6216 | copyright status | copyrighted | Q50423863 |
| P433 | issue | 5 | |
| P407 | language of work or name | English | Q1860 |
| P921 | main subject | Duchenne muscular dystrophy | Q1648484 |
| P304 | page(s) | e0213649 | |
| P577 | publication date | 2019-05-01 | |
| P1433 | published in | PLOS One | Q564954 |
| P1476 | title | Gene therapy as a potential therapeutic option for Duchenne muscular dystrophy: A qualitative preference study of patients and parents | |
| P478 | volume | 14 |
| Q90190005 | Stem Cell Aging in Skeletal Muscle Regeneration and Disease | cites work | P2860 |
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