| scholarly article | Q13442814 |
| review article | Q7318358 |
| P50 | author | Hemant Khanna | Q83233957 |
| P2093 | author name string | Lolita Petit | |
| Claudio Punzo | |||
| P2860 | cites work | X-linked IAP is a direct inhibitor of cell-death proteases | Q24318710 |
| The spatio-temporal pattern of photoreceptor degeneration in the aged rd/rd mouse retina | Q71067825 | ||
| Inhibition of retinal neovascularization by intraocular viral-mediated delivery of anti-angiogenic agents | Q78365092 | ||
| Regulation of rod phototransduction machinery by ciliary neurotrophic factor | Q79455997 | ||
| Antioxidants slow photoreceptor cell death in mouse models of retinitis pigmentosa | Q80372689 | ||
| AAV-mediated gene replacement, either alone or in combination with physical and pharmacological agents, results in partial and transient protection from photoreceptor degeneration associated with betaPDE deficiency | Q83313750 | ||
| CNGB3-Achromatopsia Clinical Trial With CNTF: Diminished Rod Pathway Responses With No Evidence of Improvement in Cone Function | Q86863683 | ||
| XIAP-mediated neuroprotection in retinal ischemia | Q45888829 | ||
| Protection of mouse photoreceptors by survival factors in retinal degenerations. | Q46022707 | ||
| Combination angiostatin and endostatin gene transfer induces synergistic antiangiogenic activity in vitro and antitumor efficacy in leukemia and solid tumors in mice | Q46618427 | ||
| Assessment of structure and function over a 3-year period after gene transfer in RPE65-/- dogs | Q46963873 | ||
| Repeated injections of a ciliary neurotrophic factor analogue leading to long-term photoreceptor survival in hereditary retinal degeneration. | Q48217416 | ||
| Systemic gene delivery protects the photoreceptors in the retinal degeneration slow mouse. | Q50539526 | ||
| CNTF gene transfer protects ganglion cells in rat retinae undergoing focal injury and branch vessel occlusion. | Q53612438 | ||
| Photoreceptor degeneration and synaptogenesis in retinal-degenerative (rd) mice | Q53737559 | ||
| Rod-cone dysplasia (progressive retinal atrophy) in Irish setters | Q66909699 | ||
| Retinal degenerations in the dog III abnormal cyclic nucleotide metabolism in rod-cone dysplasia | Q67255562 | ||
| Inhibition of vascular endothelial cell growth factor activity by an endogenously encoded soluble receptor | Q24320710 | ||
| RPE65 is the isomerohydrolase in the retinoid visual cycle | Q24530226 | ||
| The c-IAP-1 and c-IAP-2 proteins are direct inhibitors of specific caspases | Q24532851 | ||
| Inactivation of the murine X-linked juvenile retinoschisis gene, Rs1h, suggests a role of retinoschisin in retinal cell layer organization and synaptic structure | Q24534221 | ||
| Allosteric control of an ionotropic glutamate receptor with an optical switch. | Q24544302 | ||
| Ectopic expression of a microbial-type rhodopsin restores visual responses in mice with photoreceptor degeneration | Q24547085 | ||
| Expression in cochlea and retina of myosin VIIa, the gene product defective in Usher syndrome type 1B | Q24562934 | ||
| Gene therapy rescues cone function in congenital achromatopsia | Q24595787 | ||
| Treatment of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trial | Q24608049 | ||
| Longitudinal study of cone photoreceptors during retinal degeneration and in response to ciliary neurotrophic factor treatment | Q24611007 | ||
| Correction of the disease phenotype in the mouse model of Stargardt disease by lentiviral gene therapy | Q24621941 | ||
| Safety and efficacy of gene transfer for Leber's congenital amaurosis | Q24634724 | ||
| New Diagnostic and Therapeutic Approaches for Preventing the Progression of Diabetic Retinopathy | Q26765468 | ||
| Optogenetics: 10 years of microbial opsins in neuroscience | Q26797268 | ||
| Age-Related Macular Degeneration: Advances in Management and Diagnosis | Q26799617 | ||
| Promising and delivering gene therapies for vision loss | Q27007079 | ||
| Gene therapy of inherited retinal degenerations: prospects and challenges | Q27009261 | ||
| A comprehensive review of retinal gene therapy | Q27023914 | ||
| Optogenetic Vision Restoration Using Rhodopsin for Enhanced Sensitivity | Q27318230 | ||
| Gene Augmentation Therapy Restores Retinal Function and Visual Behavior in a Sheep Model of CNGA3 Achromatopsia | Q27318262 | ||
| Dosage thresholds for AAV2 and AAV8 photoreceptor gene therapy in monkey | Q27329160 | ||
| Pigment epithelium-derived factor: a potent inhibitor of angiogenesis | Q28139159 | ||
| Pigment epithelium-derived factor inhibits retinal and choroidal neovascularization | Q28203561 | ||
| Evaluation of retinal photoreceptors and pigment epithelium in a female carrier of choroideremia | Q28211660 | ||
| Selective photostimulation of genetically chARGed neurons | Q28214704 | ||
| Restoration of vision in the pde6β-deficient dog, a large animal model of rod-cone dystrophy | Q28271734 | ||
| Effect of gene therapy on visual function in Leber's congenital amaurosis | Q28277981 | ||
| Photoreceptor cell rescue in retinal degeneration (rd) mice by in vivo gene therapy | Q28279907 | ||
| Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial. | Q28306059 | ||
| RS-1 Gene Delivery to an Adult Rs1h Knockout Mouse Model Restores ERG b-Wave with Reversal of the Electronegative Waveform of X-Linked Retinoschisis | Q28506399 | ||
| Restoration of cone vision in a mouse model of achromatopsia | Q28509747 | ||
| CNTF promotes survival of retinal ganglion cells after induction of ocular hypertension in rats: the possible involvement of STAT3 pathway | Q28568156 | ||
| A unified model for apical caspase activation | Q28609101 | ||
| Gene Therapy Fully Restores Vision to the All-Cone Nrl(-/-) Gucy2e(-/-) Mouse Model of Leber Congenital Amaurosis-1. | Q36074089 | ||
| Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors | Q36099346 | ||
| Halting progressive neurodegeneration in advanced retinitis pigmentosa | Q36106057 | ||
| Intravitreal Ciliary Neurotrophic Factor Transiently Improves Cone-Mediated Function in a CNGB3-/- Mouse Model of Achromatopsia | Q36232212 | ||
| Outcome measures and their application in clinical trials for retinal degenerative diseases: outline, review, and perspective. | Q36248832 | ||
| Proinsulin slows retinal degeneration and vision loss in the P23H rat model of retinitis pigmentosa | Q36469478 | ||
| Gene therapy provides long-term visual function in a pre-clinical model of retinitis pigmentosa | Q36525867 | ||
| Cone-Specific Promoters for Gene Therapy of Achromatopsia and Other Retinal Diseases | Q36543458 | ||
| ω-3 intake and visual acuity in patients with retinitis pigmentosa receiving vitamin A | Q36554776 | ||
| Human retinal gene therapy for Leber congenital amaurosis shows advancing retinal degeneration despite enduring visual improvement | Q36598421 | ||
| AAV-mediated gene therapy in the guanylate cyclase (RetGC1/RetGC2) double knockout mouse model of Leber congenital amaurosis. | Q36635482 | ||
| AAV-mediated gene therapy for retinal degeneration in the rd10 mouse containing a recessive PDEbeta mutation | Q36678695 | ||
| Long-term restoration of rod and cone vision by single dose rAAV-mediated gene transfer to the retina in a canine model of childhood blindness | Q36825024 | ||
| AAV-mediated transduction and targeting of retinal bipolar cells with improved mGluR6 promoters in rodents and primates | Q36890213 | ||
| Transient photoreceptor deconstruction by CNTF enhances rAAV-mediated cone functional rescue in late stage CNGB3-achromatopsia | Q36915103 | ||
| Two mouse retinal degenerations caused by missense mutations in the beta-subunit of rod cGMP phosphodiesterase gene | Q36926146 | ||
| Human gene therapy for RPE65 isomerase deficiency activates the retinoid cycle of vision but with slow rod kinetics | Q36937189 | ||
| Improved cell metabolism prolongs photoreceptor survival upon retinal-pigmented epithelium loss in the sodium iodate induced model of geographic atrophy | Q36962720 | ||
| Versatility of AAV vectors for retinal gene transfer | Q36965152 | ||
| Retinal organization in the retinal degeneration 10 (rd10) mutant mouse: a morphological and ERG study | Q36990099 | ||
| XIAP effects on retinal detachment-induced photoreceptor apoptosis [corrected]. | Q37024493 | ||
| Visual Acuity after Retinal Gene Therapy for Choroideremia. | Q37200664 | ||
| The thioredoxin-like protein rod-derived cone viability factor (RdCVFL) interacts with TAU and inhibits its phosphorylation in the retina | Q37212463 | ||
| IQCB1 and PDE6B mutations cause similar early onset retinal degenerations in two closely related terrier dog breeds | Q37259774 | ||
| Functional rescue of degenerating photoreceptors in mice homozygous for a hypomorphic cGMP phosphodiesterase 6 b allele (Pde6bH620Q). | Q37273993 | ||
| Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1: effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors | Q37292973 | ||
| Combined rod and cone transduction by adeno-associated virus 2/8. | Q37404344 | ||
| Mid-stage intervention achieves similar efficacy as conventional early-stage treatment using gene therapy in a pre-clinical model of retinitis pigmentosa | Q37406449 | ||
| Intravitreal delivery of AAV8 retinoschisin results in cell type-specific gene expression and retinal rescue in the Rs1-KO mouse | Q37414094 | ||
| Tyrosine capsid-mutant AAV vectors for gene delivery to the canine retina from a subretinal or intravitreal approach | Q37432588 | ||
| New photochemical tools for controlling neuronal activity. | Q37458531 | ||
| Lighting a candle in the dark: advances in genetics and gene therapy of recessive retinal dystrophies | Q37784661 | ||
| The melanopsin system: Phototransduction, projections, functions, and clinical implications | Q37866574 | ||
| Novel adeno-associated viral vectors for retinal gene therapy | Q37944999 | ||
| Loss of daylight vision in retinal degeneration: are oxidative stress and metabolic dysregulation to blame? | Q37954832 | ||
| AAV-mediated cone rescue in a naturally occurring mouse model of CNGA3-achromatopsia | Q28730645 | ||
| Treatment of retinitis pigmentosa due to MERTK mutations by ocular subretinal injection of adeno-associated virus gene vector: results of a phase I trial | Q30277652 | ||
| Restoration of cone vision in the CNGA3-/- mouse model of congenital complete lack of cone photoreceptor function | Q30497586 | ||
| The human rhodopsin kinase promoter in an AAV5 vector confers rod- and cone-specific expression in the primate retina. | Q30525669 | ||
| Gene therapy for leber congenital amaurosis caused by RPE65 mutations: safety and efficacy in 15 children and adults followed up to 3 years | Q30537764 | ||
| Successful gene therapy in the RPGRIP1-deficient dog: a large model of cone-rod dystrophy | Q30571313 | ||
| AAV2 gene therapy readministration in three adults with congenital blindness. | Q30587265 | ||
| Restoration of visual function by expression of a light-gated mammalian ion channel in retinal ganglion cells or ON-bipolar cells | Q30612156 | ||
| Gene therapy restores vision in rd1 mice after removal of a confounding mutation in Gpr179 | Q30626026 | ||
| Potential long-term inhibition of ocular neovascularisation by recombinant adeno-associated virus-mediated secretion gene therapy | Q31065469 | ||
| AAV-mediated delivery of ciliary neurotrophic factor prolongs photoreceptor survival in the rhodopsin knockout mouse | Q32125104 | ||
| XIAP protection of photoreceptors in animal models of retinitis pigmentosa | Q33279531 | ||
| Reversal of blindness in animal models of leber congenital amaurosis using optimized AAV2-mediated gene transfer | Q33315634 | ||
| Effect of CNTF on retinal ganglion cell survival in experimental glaucoma | Q33390314 | ||
| Adeno-associated vector (type 8)-mediated expression of soluble Flt-1 efficiently inhibits neovascularization in a murine choroidal neovascularization model | Q33522293 | ||
| Increased expression of catalase and superoxide dismutase 2 reduces cone cell death in retinitis pigmentosa | Q33579158 | ||
| Gene therapy with a promoter targeting both rods and cones rescues retinal degeneration caused by AIPL1 mutations | Q33584461 | ||
| Functional and behavioral restoration of vision by gene therapy in the guanylate cyclase-1 (GC1) knockout mouse. | Q33622429 | ||
| Functional cone rescue by RdCVF protein in a dominant model of retinitis pigmentosa | Q33713504 | ||
| Evidence for the failure of adeno-associated virus serotype 5 to package a viral genome > or = 8.2 kb. | Q33730469 | ||
| The Inheritance of a Retinal Abnormality in White Mice | Q33764266 | ||
| Randomized trial of ciliary neurotrophic factor delivered by encapsulated cell intraocular implants for retinitis pigmentosa | Q33953997 | ||
| Identification and characterization of rod-derived cone viability factor | Q33979422 | ||
| Leber congenital amaurosis due to RPE65 mutations and its treatment with gene therapy | Q33992484 | ||
| Mutation of key residues of RPE65 abolishes its enzymatic role as isomerohydrolase in the visual cycle. | Q34015881 | ||
| Genetic reactivation of cone photoreceptors restores visual responses in retinitis pigmentosa | Q34022879 | ||
| Optogenetic therapy for retinitis pigmentosa | Q34028956 | ||
| Gene therapy for blindness | Q34037010 | ||
| Replacement gene therapy with a human RPGRIP1 sequence slows photoreceptor degeneration in a murine model of Leber congenital amaurosis | Q34085940 | ||
| Independent degeneration of photoreceptors and retinal pigment epithelium in conditional knockout mouse models of choroideremia | Q34249600 | ||
| Clinical trial of lutein in patients with retinitis pigmentosa receiving vitamin A | Q34330189 | ||
| Efficient transduction and optogenetic stimulation of retinal bipolar cells by a synthetic adeno-associated virus capsid and promoter. | Q34342494 | ||
| A randomized trial of vitamin A and vitamin E supplementation for retinitis pigmentosa | Q34366637 | ||
| Optochemical genetics | Q37959926 | ||
| Retinal cell death and current strategies in retinal neuroprotection. | Q38194848 | ||
| The Status of RPE65 Gene Therapy Trials: Safety and Efficacy | Q38337392 | ||
| Rod-derived cone viability factor promotes cone survival by stimulating aerobic glycolysis | Q38886238 | ||
| Long-term preservation of cones and improvement in visual function following gene therapy in a mouse model of leber congenital amaurosis caused by guanylate cyclase-1 deficiency. | Q38899558 | ||
| AAV-mediated Gene Therapy Halts Retinal Degeneration in PDE6β-deficient Dogs | Q38910623 | ||
| Rescue from photoreceptor degeneration in the rd mouse by human immunodeficiency virus vector-mediated gene transfer | Q39551137 | ||
| Investor Outlook: Significance of the Positive LCA2 Gene Therapy Phase III Results | Q40192758 | ||
| In vivo gene therapy in young and adult RPE65-/- dogs produces long-term visual improvement. | Q40594379 | ||
| Potential synergistic protection of retinal ganglion cells from axotomy-induced apoptosis by adenoviral administration of glial cell line-derived neurotrophic factor and X-chromosome-linked inhibitor of apoptosis | Q40686217 | ||
| Encapsulated cell-based delivery of CNTF reduces photoreceptor degeneration in animal models of retinitis pigmentosa. | Q40700552 | ||
| Results at 2 Years after Gene Therapy for RPE65-Deficient Leber Congenital Amaurosis and Severe Early-Childhood-Onset Retinal Dystrophy. | Q40787452 | ||
| Encapsidated adenovirus mini-chromosome-mediated delivery of genes to the retina: application to the rescue of photoreceptor degeneration | Q40995318 | ||
| Gene therapy with recombinant adeno-associated vectors for neovascular age-related macular degeneration: 1 year follow-up of a phase 1 randomised clinical trial | Q41269839 | ||
| Intravitreal delivery of a novel AAV vector targets ON bipolar cells and restores visual function in a mouse model of complete congenital stationary night blindness | Q41449349 | ||
| Gene therapy in the second eye of RPE65-deficient dogs improves retinal function | Q41835416 | ||
| Retinal gene therapy coming of age | Q41855035 | ||
| Stimulation of the insulin/mTOR pathway delays cone death in a mouse model of retinitis pigmentosa | Q41967871 | ||
| Virally delivered channelrhodopsin-2 safely and effectively restores visual function in multiple mouse models of blindness | Q41991320 | ||
| Light-driven cone arrestin translocation in cones of postnatal guanylate cyclase-1 knockout mouse retina treated with AAV-GC1. | Q42006936 | ||
| Preclinical safety evaluation of AAV2-sFLT01- a gene therapy for age-related macular degeneration | Q42123516 | ||
| Gene therapy restores vision and delays degeneration in the CNGB1(-/-) mouse model of retinitis pigmentosa. | Q42229312 | ||
| Successful gene therapy in older Rpe65-deficient dogs following subretinal injection of an adeno-associated vector expressing RPE65. | Q42270262 | ||
| Non-erythropoietic erythropoietin derivatives protect from light-induced and genetic photoreceptor degeneration. | Q42729265 | ||
| Photochemical tools to study dynamic biological processes | Q42945168 | ||
| Visual function in mice with photoreceptor degeneration and transgenic expression of channelrhodopsin 2 in ganglion cells. | Q42997869 | ||
| mTORC1 sustains vision in retinitis pigmentosa | Q43195494 | ||
| Adeno-associated virus-mediated rhodopsin replacement provides therapeutic benefit in mice with a targeted disruption of the rhodopsin gene. | Q43262568 | ||
| Prolonged recovery of retinal structure/function after gene therapy in an Rs1h-deficient mouse model of x-linked juvenile retinoschisis | Q43534316 | ||
| Lentiviral vector-mediated gene transfer in adult mouse photoreceptors is impaired by the presence of a physical barrier | Q43564494 | ||
| Gene therapy restores vision in a canine model of childhood blindness | Q43590733 | ||
| Differential effect of the rd mutation on rods and cones in the mouse retina | Q43641682 | ||
| Baculoviral IAP repeat-containing-4 protects optic nerve axons in a rat glaucoma model | Q44003999 | ||
| Effects of adeno-associated virus-vectored ciliary neurotrophic factor on retinal structure and function in mice with a P216L rds/peripherin mutation | Q44070483 | ||
| Periocular gene transfer of sFlt-1 suppresses ocular neovascularization and vascular endothelial growth factor-induced breakdown of the blood-retinal barrier | Q44340120 | ||
| Intraocular gene delivery of ciliary neurotrophic factor results in significant loss of retinal function in normal mice and in the Prph2Rd2/Rd2 model of retinal degeneration | Q44351246 | ||
| Functional and structural recovery of the retina after gene therapy in the RPE65 null mutation dog. | Q44376450 | ||
| The X-linked inhibitor of apoptosis (XIAP) prevents cell death in axotomized CNS neurons in vivo. | Q44413676 | ||
| Structural and functional protection of photoreceptors from MNU-induced retinal degeneration by the X-linked inhibitor of apoptosis | Q44453160 | ||
| Effect of late-stage therapy on disease progression in AAV-mediated rescue of photoreceptor cells in the retinoschisin-deficient mouse | Q44690695 | ||
| Rescue of photoreceptor function by AAV-mediated gene transfer in a mouse model of inherited retinal degeneration | Q44933268 | ||
| Marked inhibition of retinal neovascularization in rats following soluble-flt-1 gene transfer | Q45047728 | ||
| Systemic but not intraocular Epo gene transfer protects the retina from light-and genetic-induced degeneration | Q45127739 | ||
| Ciliary neurotrophic factor protects retinal ganglion cells from secondary cell death during acute autoimmune optic neuritis in rats | Q45191522 | ||
| Oxidative damage is a potential cause of cone cell death in retinitis pigmentosa | Q45297114 | ||
| In vivo-directed evolution of a new adeno-associated virus for therapeutic outer retinal gene delivery from the vitreous | Q45350780 | ||
| AAV-mediated expression of CNTF promotes long-term survival and regeneration of adult rat retinal ganglion cells | Q45858441 | ||
| Restoration of vision in RPE65-deficient Briard dogs using an AAV serotype 4 vector that specifically targets the retinal pigmented epithelium | Q45863029 | ||
| Prevention of diabetic retinopathy by intraocular soluble flt-1 gene transfer in a spontaneously diabetic rat model. | Q45864206 | ||
| AAV-mediated expression targeting of rod and cone photoreceptors with a human rhodopsin kinase promoter | Q45870501 | ||
| RPE65 gene therapy slows cone loss in Rpe65-deficient dogs | Q45881587 | ||
| Gene replacement therapy rescues photoreceptor degeneration in a murine model of Leber congenital amaurosis lacking RPGRIP. | Q45886246 | ||
| Retinal optogenetic therapies: clinical criteria for candidacy | Q45886746 | ||
| Ciliary neurotrophic factor (CNTF) for human retinal degeneration: phase I trial of CNTF delivered by encapsulated cell intraocular implants | Q34410761 | ||
| Improvement and decline in vision with gene therapy in childhood blindness. | Q34474831 | ||
| Successful arrest of photoreceptor and vision loss expands the therapeutic window of retinal gene therapy to later stages of disease | Q34497784 | ||
| G proteins and phototransduction. | Q34516163 | ||
| Long-term retinal function and structure rescue using capsid mutant AAV8 vector in the rd10 mouse, a model of recessive retinitis pigmentosa. | Q34556959 | ||
| Lentiviral gene replacement therapy of retinas in a mouse model for Usher syndrome type 1B. | Q34608354 | ||
| Targeting channelrhodopsin-2 to ON-bipolar cells with vitreally administered AAV Restores ON and OFF visual responses in blind mice | Q34734029 | ||
| Light-activated channels targeted to ON bipolar cells restore visual function in retinal degeneration | Q34773506 | ||
| Ciliary neurotrophic factor delivered by encapsulated cell intraocular implants for treatment of geographic atrophy in age-related macular degeneration | Q34794630 | ||
| Restoration of visual function in retinal degeneration mice by ectopic expression of melanopsin. | Q34845685 | ||
| Antioxidants reduce cone cell death in a model of retinitis pigmentosa | Q34983972 | ||
| LiGluR restores visual responses in rodent models of inherited blindness | Q35086097 | ||
| AAV5-mediated sFLT01 gene therapy arrests retinal lesions in Ccl2(-/-)/Cx3cr1(-/-) mice | Q35106359 | ||
| Long-term and age-dependent restoration of visual function in a mouse model of CNGB3-associated achromatopsia following gene therapy | Q35119686 | ||
| EIAV-based retinal gene therapy in the shaker1 mouse model for usher syndrome type 1B: development of UshStat | Q35140281 | ||
| Genetic deletion of S-opsin prevents rapid cone degeneration in a mouse model of Leber congenital amaurosis | Q35152826 | ||
| Overexpression of SOD in retina: need for increase in H2O2-detoxifying enzyme in same cellular compartment | Q35186292 | ||
| Viral-mediated RdCVF and RdCVFL expression protects cone and rod photoreceptors in retinal degeneration | Q35242633 | ||
| NRF2 promotes neuronal survival in neurodegeneration and acute nerve damage | Q35408649 | ||
| Activated mTORC1 promotes long-term cone survival in retinitis pigmentosa mice | Q35409026 | ||
| Long-term preservation of cone photoreceptors and restoration of cone function by gene therapy in the guanylate cyclase-1 knockout (GC1KO) mouse. | Q35518971 | ||
| Gene therapy using self-complementary Y733F capsid mutant AAV2/8 restores vision in a model of early onset Leber congenital amaurosis | Q35532922 | ||
| Efficient gene delivery to photoreceptors using AAV2/rh10 and rescue of the Rho(-/-) mouse | Q35651062 | ||
| Gene therapy rescues photoreceptor blindness in dogs and paves the way for treating human X-linked retinitis pigmentosa | Q35751018 | ||
| Long-term effect of gene therapy on Leber's congenital amaurosis | Q35836291 | ||
| CNTF Gene Therapy Confers Lifelong Neuroprotection in a Mouse Model of Human Retinitis Pigmentosa | Q35964344 | ||
| Synaptic pathology and therapeutic repair in adult retinoschisis mouse by AAV-RS1 transfer | Q36040298 | ||
| P275 | copyright license | Creative Commons Attribution-NonCommercial | Q6936496 |
| P433 | issue | 8 | |
| P407 | language of work or name | English | Q1860 |
| P921 | main subject | gene therapy | Q213901 |
| eye disease | Q3041498 | ||
| biomedical investigative technique | Q66648976 | ||
| P5008 | on focus list of Wikimedia project | ScienceSource | Q55439927 |
| P304 | page(s) | 563-579 | |
| P577 | publication date | 2016-05-13 | |
| 2016-08-01 | |||
| P1433 | published in | Human Gene Therapy | Q15757580 |
| P1476 | title | Advances in Gene Therapy for Diseases of the Eye. | |
| P478 | volume | 27 |
| Q57819244 | A Destabilizing Domain Allows for Fast, Noninvasive, Conditional Control of Protein Abundance in the Mouse Eye - Implications for Ocular Gene Therapy |
| Q36396453 | AAV-Mediated Gene Supplementation Therapy in Achromatopsia Type 2: Preclinical Data on Therapeutic Time Window and Long-Term Effects |
| Q47556217 | AAV-mediated gene delivery of the calreticulin anti-angiogenic domain inhibits ocular neovascularization |
| Q64040883 | Adeno-associated virus vector as a platform for gene therapy delivery |
| Q89993054 | Advanced Formulation Approaches for Ocular Drug Delivery: State-Of-The-Art and Recent Patents |
| Q55274674 | Aerobic Glycolysis Is Essential for Normal Rod Function and Controls Secondary Cone Death in Retinitis Pigmentosa. |
| Q104064500 | CCDC66 frameshift variant associated with a new form of early-onset progressive retinal atrophy in Portuguese Water Dogs |
| Q90437695 | Complex Structural PPT1 Variant Associated with Non-syndromic Canine Retinal Degeneration |
| Q40134387 | Gene Therapy Using a miniCEP290 Fragment Delays Photoreceptor Degeneration in a Mouse Model of Leber Congenital Amaurosis |
| Q58779270 | Human Vascular Endothelial Growth Factor A Expression Induces the Mouse Model of Neovascular Age-Related Macular Degeneration |
| Q47168463 | Involvement of Innate Immune System in Late Stages of Inherited Photoreceptor Degeneration |
| Q49758178 | OPA1 gene therapy prevents retinal ganglion cell loss in a Dominant Optic Atrophy mouse model. |
| Q64376752 | Photobiomodulation promotes adenoviral gene transduction in auditory cells |
| Q33846303 | Rod Outer Segment Development Influences AAV-Mediated Photoreceptor Transduction After Subretinal Injection |
| Q45872446 | The clinical implications of molecular monitoring and analyses of inherited retinal diseases |
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