CRISPR/Cas9-mediated genome engineering: an adeno-associated viral (AAV) vector toolbox

scientific article published on 6 October 2014

CRISPR/Cas9-mediated genome engineering: an adeno-associated viral (AAV) vector toolbox is …
instance of (P31):
scholarly articleQ13442814

External links are
P356DOI10.1002/BIOT.201400046
P698PubMed publication ID25186301

P50authorDirk GrimmQ67484042
Kathleen BörnerQ98389411
Ellen WiedtkeQ115599734
P2093author name stringAnn-Kristin Mueller
Chronis Fatouros
Dominik Niopek
Stefanie Große
Elena Senís
P2860cites workDNA DSB repair pathway choice: an orchestrated handover mechanismQ26861805
Functional repair of CFTR by CRISPR/Cas9 in intestinal stem cell organoids of cystic fibrosis patientsQ28303521
One-step generation of mice carrying mutations in multiple genes by CRISPR/Cas-mediated genome engineeringQ29547524
RNA-guided genetic silencing systems in bacteria and archaeaQ29614421
CRISPR-Cas systems for editing, regulating and targeting genomesQ29615781
Dynamic imaging of genomic loci in living human cells by an optimized CRISPR/Cas systemQ29615782
Repurposing CRISPR as an RNA-guided platform for sequence-specific control of gene expressionQ29615784
Improving CRISPR-Cas nuclease specificity using truncated guide RNAsQ29616043
Genome-scale CRISPR-Cas9 knockout screening in human cellsQ29616044
Genetic screens in human cells using the CRISPR-Cas9 systemQ29617411
Argonaute proteins are key determinants of RNAi efficacy, toxicity, and persistence in the adult mouse liverQ30434933
Genome-wide analysis reveals characteristics of off-target sites bound by the Cas9 endonuclease.Q30458169
Random peptide libraries displayed on adeno-associated virus to select for targeted gene therapy vectorsQ30975099
In vitro and in vivo gene therapy vector evolution via multispecies interbreeding and retargeting of adeno-associated virusesQ33327474
Oligomerized pool engineering (OPEN): an 'open-source' protocol for making customized zinc-finger arraysQ33508083
Low incidence of off-target mutations in individual CRISPR-Cas9 and TALEN targeted human stem cell clones detected by whole-genome sequencing.Q33849553
ZiFiT (Zinc Finger Targeter): an updated zinc finger engineering toolQ33957629
Genome-wide binding of the CRISPR endonuclease Cas9 in mammalian cellsQ34093413
High-efficiency transduction of fibroblasts and mesenchymal stem cells by tyrosine-mutant AAV2 vectors for their potential use in cellular therapyQ34329364
The tracrRNA and Cas9 families of type II CRISPR-Cas immunity systemsQ34337685
Fatality in mice due to oversaturation of cellular microRNA/short hairpin RNA pathwaysQ34530552
Production methods for gene transfer vectors based on adeno-associated virus serotypesQ34987161
From virus evolution to vector revolution: use of naturally occurring serotypes of adeno-associated virus (AAV) as novel vectors for human gene therapyQ35180997
Adenovirus-associated virus vector-mediated gene transfer in hemophilia BQ35691659
Robust RNAi enhancement via human Argonaute-2 overexpression from plasmids, viral vectors and cell linesQ37327641
Analysis of off-target effects of CRISPR/Cas-derived RNA-guided endonucleases and nickases.Q37420333
A guide to genome engineering with programmable nucleasesQ38201212
Gene therapy for inherited retinal degenerationsQ38202230
Current status of haemophilia gene therapyQ38206852
Efficient gene delivery to the cone-enriched pig retina by dual AAV vectorsQ42235082
Targeted gene disruption in somatic zebrafish cells using engineered TALENsQ42862072
Preclinical in vivo evaluation of pseudotyped adeno-associated virus vectors for liver gene therapyQ44976981
Novel tools for production and purification of recombinant adenoassociated virus vectorsQ45752072
Human Argonaute2 mediates RNA cleavage targeted by miRNAs and siRNAsQ24299641
Cas9 as a versatile tool for engineering biologyQ24564294
RNA-guided human genome engineering via Cas9Q24598394
Multiplex genome engineering using CRISPR/Cas systemsQ24609428
Efficient genome editing in zebrafish using a CRISPR-Cas systemQ24610828
Genome engineering in Saccharomyces cerevisiae using CRISPR-Cas systemsQ24633670
A Programmable Dual-RNA-Guided DNA Endonuclease in Adaptive Bacterial ImmunityQ24669850
P433issue11
P921main subjectCRISPRQ412563
Cas9Q16965677
P304page(s)1402-1412
P577publication date2014-10-06
P1433published inBiotechnology JournalQ15716480
P1476titleCRISPR/Cas9-mediated genome engineering: an adeno-associated viral (AAV) vector toolbox
P478volume9

Reverse relations

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