AAV vectors: is clinical success on the horizon?

scientific article

AAV vectors: is clinical success on the horizon? is …
instance of (P31):
review articleQ7318358
scholarly articleQ13442814

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P356DOI10.1038/SJ.GT.3301109
P698PubMed publication ID10680012
P5875ResearchGate publication ID12635477

P2093author name stringSamulski RJ
Monahan PE
P2860cites workAdeno-associated virus-mediated delivery of erythropoietin leads to sustained elevation of hematocrit in nonhuman primatesQ45753061
In vitro packaging of an infectious recombinant adeno-associated virus 2.Q45758631
Recombinant adeno-associated virus for muscle directed gene therapyQ45764433
Gene transfer into hematopoietic progenitor cells mediated by an adeno-associated virus vectorQ45842008
Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vectorQ45855552
Viral receptors and vector purification: new approaches for generating clinical-grade reagentsQ45857978
Persistent expression of canine factor IX in hemophilia B caninesQ45862802
Ribozyme rescue of photoreceptor cells in a transgenic rat model of autosomal dominant retinitis pigmentosa.Q45888779
NIDDK Workshop on AAV Vectors: Gene Transfer into Quiescent CellsQ71670224
Efficient and persistent gene transfer of AAV-CFTR in maxillary sinusQ77292224
Latent adeno-associated virus infection elicits humoral but not cell-mediated immune responses in a nonhuman primate modelQ24527302
Progress in adeno-associated virus type 2 vector production: promises and prospects for clinical use.Q33763911
Infectious clones and vectors derived from adeno-associated virus (AAV) serotypes other than AAV type 2.Q33781976
Transduction of dendritic cells by DNA viral vectors directs the immune response to transgene products in muscle fibersQ33782809
Recombinant human parvovirus B19 vectors: erythroid cell-specific delivery and expression of transduced genesQ33784686
Concatamerization of adeno-associated virus circular genomes occurs through intermolecular recombination.Q33823450
Immune responses to adenovirus and adeno-associated virus in humans.Q33874473
Insertional mutagenesis of AAV2 capsid and the production of recombinant virusQ33883772
Human fibroblast growth factor receptor 1 is a co-receptor for infection by adeno-associated virus 2.Q34486856
Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vectorQ35872651
Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic proteinQ35943644
Efficient expression of CFTR function with adeno-associated virus vectors that carry shortened CFTR genesQ36287507
Sustained correction of bleeding disorder in hemophilia B mice by gene therapyQ36454880
Sustained secretion of human alpha-1-antitrypsin from murine muscle transduced with adeno-associated virus vectorsQ36734619
High-titer recombinant adeno-associated virus production utilizing a recombinant herpes simplex virus type I vector expressing AAV-2 Rep and Cap.Q40933793
High-titer adeno-associated viral vectors from a Rep/Cap cell line and hybrid shuttle virusQ40992577
Nucleotide sequencing and generation of an infectious clone of adeno-associated virus 3.Q41190212
Genetic capsid modifications allow efficient re-targeting of adeno-associated virus type 2.Q42609041
Titration of AAV-2 particles via a novel capsid ELISA: packaging of genomes can limit production of recombinant AAV-2.Q43567043
Transduction and utility of the granulocyte-macrophage colony-stimulating factor gene into monocytes and dendritic cells by adeno-associated virus.Q45744533
Recombinant adeno-associated virus purification using novel methods improves infectious titer and yieldQ45747699
Highly purified recombinant adeno-associated virus vectors are biologically active and free of detectable helper and wild-type virusesQ45749766
P433issue1
P304page(s)24-30
P577publication date2000-01-01
P1433published inGene TherapyQ15763095
P1476titleAAV vectors: is clinical success on the horizon?
P478volume7

Reverse relations

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